Jenny McIntosh

Adeno-Associated Viral Vector Mediated Gene Transfer for Hemophilia B

Amit C. Nathwani, Egd Tuddenham, Andrew M. Davidoff, 2011 .

Long-term safety and efficacy of factor IX gene therapy in hemophilia B.

Michael Recht, Pratima Chowdary, Deepak Raj, 2014, The New England journal of medicine.

Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors.

Mark Basche, Jenny McIntosh, Tiansen Li, 2009, Human molecular genetics.

Recombinant adeno-associated virus-mediated in utero gene transfer gives therapeutic transgene expression in the sheep.

Anna L David, Michael Boyd, Simon Waddington, 2011, Human gene therapy.

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver.

Geoffrey Kemball-Cook, Jenny McIntosh, Yunyu Spence, 2006, Blood.

Adenovirus-associated virus vector-mediated gene transfer in hemophilia B.

Pratima Chowdary, Savita Rangarajan, Cecilia Rosales, 2011, The New England journal of medicine.