Christian Brendel

Transient expression of LEDGF-chimera results in retargeted and safer lentiviral vector integration

Zeger Debyser, Rik Gijsbers, Manuel Grez, 2013 .

Highly efficient therapeutic gene editing of human hematopoietic stem cells

Chunyan Ren, Luca Pinello, Luca Biasco, 2019, Nature Medicine.

Editing aberrant splice sites efficiently restores β-globin expression in β-thalassemia.

Luca Pinello, Kevin Luk, Scot A Wolfe, 2019, Blood.

miRNA-embedded shRNAs for Lineage-specific BCL11A Knockdown and Hemoglobin F Induction.

Matthew C. Canver, David A. Williams, Matthew C Canver, 2015, Molecular therapy : the journal of the American Society of Gene Therapy.