Nathan Katz

发表

Exome-by-phenome-wide rare variant gene burden association with electronic health record phenotypes

Jinbo Chen, D. Rader, M. Ritchie, 2019, bioRxiv.

Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model.

James M. Wilson, Nathan Katz, M. Haskins, 2016, Molecular genetics and metabolism.

Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques

James M. Wilson, Nathan Katz, R. Calcedo, 2018, Molecular therapy. Methods & clinical development.

A Single Injection of an Optimized Adeno-Associated Viral Vector into Cerebrospinal Fluid Corrects Neurological Disease in a Murine Model of GM1 Gangliosidosis

James M. Wilson, Nathan Katz, Christian Hinderer, 2020, Human gene therapy.

Evaluation of Intrathecal Routes of Administration for Adeno-Associated Viral Vectors in Large Animals.

C. Vite, James M. Wilson, Nathan Katz, 2018, Human gene therapy.

Translational Feasibility of Lumbar Puncture for Intrathecal AAV Administration

James M. Wilson, Nathan Katz, P. Bell, 2020, Molecular therapy. Methods & clinical development.

Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN.

James M. Wilson, Nathan Katz, P. Bell, 2018, Human gene therapy.

Standardized Method for Intra-Cisterna Magna Delivery Under Fluoroscopic Guidance in Nonhuman Primates.

James M. Wilson, Nathan Katz, J. Hordeaux, 2018, Human gene therapy methods.

Abnormal polyamine metabolism is unique to the neuropathic forms of MPS: potential for biomarker development and insight into pathogenesis

J. Tolar, James M. Wilson, C. Mesaros, 2017, Human molecular genetics.

Manganese homeostasis: from rare single-gene disorders to complex phenotypes and diseases.

D. Rader, Nathan Katz, 2019, The Journal of clinical investigation.

The Neurotropic Properties of AAV-PHP.B Are Limited to C57BL/6J Mice.

Qiang Wang, Peter Bell, James M. Wilson, 2018, Molecular therapy : the journal of the American Society of Gene Therapy.

Exome-wide evaluation of rare coding variants using electronic health records identifies new gene–phenotype associations

Alexander Hanbo Li, Judy H. Cho, K. Kaestner, 2021, Nature Medicine.

Delivery of an Adeno-Associated Virus Vector into Cerebrospinal Fluid Attenuates Central Nervous System Disease in Mucopolysaccharidosis Type II Mice.

James M. Wilson, Nathan Katz, Hongwei Yu, 2016, Human gene therapy.

Adeno-Associated Virus-Induced Dorsal Root Ganglion Pathology.

Mingyao Li, James M. Wilson, Nathan Katz, 2020, Human gene therapy.

A Feasibility Study on 3D Bioprinting of Microfat Constructs Towards Wound Healing Applications

Vipuil Kishore, Nathan Katz, Trevor Schmitt, 2021, Frontiers in Bioengineering and Biotechnology.

Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN.

James M. Wilson, Nathan Katz, E. Buza, 2018, Human gene therapy.