J. Morgan

发表

Muscle histology vs MRI in Duchenne muscular dystrophy

E. Mercuri, K. Bushby, F. Muntoni, 2011, Neurology.

Direct effects of the pathogenic mutation on satellite cell function in muscular dystrophy.

J. Morgan, P. Zammit, 2010, Experimental cell research.

MMP‐9 overexpression improves myogenic cell migration and engraftment

M. Fiszman, J. Morgan, H. Alameddine, 2010, Muscle & nerve.

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

I. Graham, K. Bushby, F. Muntoni, 2009, The Lancet Neurology.

Correlation of Utrophin Levels with the Dystrophin Protein Complex and Muscle Fibre Regeneration in Duchenne and Becker Muscular Dystrophy Muscle Biopsies

K. Davies, F. Muntoni, C. Sewry, 2016, PloS one.

Revertant fibres and dystrophin traces in Duchenne muscular dystrophy: Implication for clinical trials

M. Main, K. Bushby, F. Muntoni, 2010, Neuromuscular Disorders.

Muscle satellite cells.

T. Partridge, J. Morgan, 2003, The international journal of biochemistry & cell biology.

Myostatin Is a Quantifiable Biomarker for Monitoring Pharmaco-gene Therapy in Duchenne Muscular Dystrophy

F. Muntoni, I. Barthélémy, S. Blot, 2020, Molecular therapy. Methods & clinical development.

Evidence for a myogenic stem cell that is exhausted in dystrophic muscle.

J. Morgan, L. Heslop, T. Partridge, 2000, Journal of cell science.

BMP signalling permits population expansion by preventing premature myogenic differentiation in muscle satellite cells

J. Morgan, P. Zammit, T. Katagiri, 2011, Cell Death and Differentiation.

Changes in Myonuclear Number During Postnatal Growth – Implications for AAV Gene Therapy for Muscular Dystrophy

F. Muntoni, J. Morgan, 2021, Journal of neuromuscular diseases.

Restoration of functional full-length dystrophin after intramuscular transplantation of Foamy Virus-transduced myoblasts.

F. Muntoni, J. Morgan, M. Mcclure, 2019, Human gene therapy.

Galectin‐1 Induces Skeletal Muscle Differentiation in Human Fetal Mesenchymal Stem Cells and Increases Muscle Regeneration

D. Watt, H. Mehmet, J. Chan, 2006, Stem cells.

Dystrophin quantification and clinical correlations in Becker muscular dystrophy: implications for clinical trials.

K. Bushby, F. Muntoni, K. Anthony, 2011, Brain : a journal of neurology.

Formation of skeletal muscle in vivo from the mouse C2 cell line.

F. Walsh, T. Partridge, S. Moore, 1992, Journal of cell science.

Grafting of a Single Donor Myofibre Promotes Hypertrophy in Dystrophic Mouse Muscle

J. Morgan, L. Boldrin, 2013, PloS one.

Delivery of large transgene cassettes by foamy virus vector

J. Morgan, M. Mcclure, N. Sweeney, 2017, Scientific Reports.

Recent progress in satellite cell/myoblast engraftment – relevance for therapy

J. Morgan, D. Briggs, 2013, The FEBS journal.

Regenerative capacity of skeletal muscle

J. Morgan, J. Ehrhardt, 2005, Current opinion in neurology.

Alveolar rhabdomyosarcoma-associated proteins PAX3/FOXO1A and PAX7/FOXO1A suppress the transcriptional activity of MyoD-target genes in muscle stem cells

J. Morgan, P. Zammit, F. Relaix, 2013, Oncogene.

Single fibers of skeletal muscle as a novel graft for cell transplantation to the heart.

M. Yacoub, B. Murtuza, T. Partridge, 2002, The Journal of thoracic and cardiovascular surgery.

Effects of Mini-Dystrophin on Dystrophin-Deficient, Human Skeletal Muscle-Derived Cells

J. Morgan, J. Counsell, J. Meng, 2020, International journal of molecular sciences.

Muscle satellite cells are a functionally heterogeneous population in both somite-derived and branchiomeric muscles

J. Morgan, P. Zammit, Y. Ono, 2010, Developmental biology.

The effect of the muscle environment on the regenerative capacity of human skeletal muscle stem cells

F. Muntoni, J. Morgan, R. Asfahani, 2015, Skeletal Muscle.

Human muscle precursor cell regeneration in the mouse host is enhanced by growth factors.

G. Butler-Browne, V. Mouly, J. Morgan, 2004, Human gene therapy.

Necroptosis mediates myofibre death in dystrophin-deficient mice

F. Muntoni, C. Hourde, F. Authier, 2018, Nature Communications.

The administration of antisense oligonucleotide golodirsen reduces pathological regeneration in patients with Duchenne muscular dystrophy

E. Mercuri, F. Muntoni, L. Servais, 2021, Acta neuropathologica communications.

A high–throughput digital script for multiplexed immunofluorescent analysis and quantification of sarcolemmal and sarcomeric proteins in muscular dystrophies

F. Muntoni, F. Catapano, C. Sewry, 2020, Acta Neuropathologica Communications.

Steroids in Duchenne muscular dystrophy: from clinical trials to genomic research

F. Muntoni, J. Morgan, Ivan Fisher, 2002, Neuromuscular Disorders.

240th ENMC workshop: The involvement of skeletal muscle stem cells in the pathology of muscular dystrophies 25–27 January 2019, Hoofddorp, The Netherlands

K. Patel, F. Muntoni, C. Bönnemann, 2019, Neuromuscular Disorders.

Skeletal muscle in health and disease

T. Partridge, J. Morgan, 2020, Disease Models & Mechanisms.

Myogenicity in vitro and in vivo of mouse muscle cells separated on discontinuous Percoll gradients

J. Morgan, 1988, Journal of the Neurological Sciences.

Mouse regenerating myofibers detected as false-positive donor myofibers with anti-human spectrin.

A. Rozkalne, E. Gussoni, J. Morgan, 2014, Human gene therapy.

Myoblast transfer and gene therapy in muscular dystrophies

J. Morgan, C. Pagel, C. Pagel, 1995, Microscopy research and technique.

Mature Adult Dystrophic Mouse Muscle Environment Does Not Impede Efficient Engrafted Satellite Cell Regeneration and Self‐Renewal

F. Muntoni, J. Morgan, P. Zammit, 2009, Stem cells.

Widespread Distribution and Muscle Differentiation of Human Fetal Mesenchymal Stem Cells After Intrauterine Transplantation in Dystrophic mdx Mouse

J. Chan, N. Fisk, M. Themis, 2007, Stem cells.

Myogenic cell lines derived from transgenic mice carrying a thermolabile T antigen: a model system for the derivation of tissue-specific and mutation-specific cell lines.

M. Noble, T. Partridge, M. Peckham, 1994, Developmental biology.

Thymic Myoid Cells as a Source of Cells for Myoblast Transfer

J. Morgan, J. Gross, T. Partridge, 2000, Cell transplantation.

Yields of muscle from myogenic cells implanted into young and old mdx hosts

R. M. Fletcher, T. Partridge, J. Morgan, 1996, Muscle & nerve.

THE mdx MOUSE SKELETAL MUSCLE MYOPATHY: I. A HISTOLOGICAL, MORPHOMETRIC AND BIOCHEMICAL INVESTIGATION

T. Partridge, J. Morgan, J. Sloper, 1988, Neuropathology and applied neurobiology.

Activating muscle stem cells: therapeutic potential in muscle diseases

J. Morgan, L. Boldrin, 2007, Current opinion in neurology.

Adult Stem Cells: Adult Skeletal Muscle Stem Cells

J. Morgan, J. Meng, 2014 .

Human muscle precursor cells give rise to functional satellite cells in vivo

T. Partridge, J. Morgan, C. Adkin, 2007, Neuromuscular Disorders.

M. Grounds, T. Partridge, J. Morgan, 1993, Journal of the Neurological Sciences.

Loss-of-function mutations in SCN4A cause severe foetal hypokinesia or ‘classical’ congenital myopathy

C. Krarup, F. Muntoni, P. Ruben, 2015, Brain : a journal of neurology.

A-utrophin up-regulation in mdx skeletal muscle is independent of regeneration

Andrew P. Weir, K. Davies, J. Morgan, 2004, Neuromuscular Disorders.

Optimized lentiviral vector to restore full-length dystrophin via a cell-mediated approach in a mouse model of Duchenne muscular dystrophy

F. Muntoni, L. Popplewell, J. Morgan, 2022, Molecular therapy. Methods & clinical development.

High-Throughput Digital Image Analysis Reveals Distinct Patterns of Dystrophin Expression in Dystrophinopathy Patients

F. Muntoni, V. Sardone, E. Ricci, 2021, Journal of neuropathology and experimental neurology.

OP-JNEN210096 1..11

F. Muntoni, V. Sardone, E. Ricci, 2021 .

Increased dystrophin production with golodirsen in patients with Duchenne muscular dystrophy

E. Mercuri, F. Muntoni, L. Servais, 2020, Neurology.

Comparative analysis of antisense oligonucleotide sequences targeting exon 53 of the human DMD gene: Implications for future clinical trials

I. Graham, F. Muntoni, L. Popplewell, 2010, Neuromuscular Disorders.

Adenovirus-based targeting in myoblasts is hampered by nonhomologous vector integration.

I. Graham, G. Dickson, M. Roberts, 2008, Human gene therapy.

Mural cells paint a new picture of muscle stem cells

F. Muntoni, J. Morgan, 2007, Nature Cell Biology.

Biochemical characterization of patients with in-frame or out-of-frame DMD deletions pertinent to exon 44 or 45 skipping.

V. Ricotti, K. Bushby, F. Muntoni, 2014, JAMA neurology.

The movement of muscle precursor cells between adjacent regenerating muscles in the mouse

D. Watt, J. Morgan, T. Partridge, 2004, Anatomy and Embryology.

Release of reactive oxygen and nitrogen species from contracting skeletal muscle cells. Free Radic. Biol. Med. 37:1064–1072; 2004

M. Jackson, J. Morgan, A. McArdle, 2004 .

Release of reactive oxygen and nitrogen species from contracting skeletal muscle cells.

M. Jackson, J. Morgan, A. McArdle, 2004, Free radical biology & medicine.

Prednisolone‐induced changes in dystrophic skeletal muscle

E. Hoffman, F. Muntoni, J. Morgan, 2005, FASEB journal : official publication of the Federation of American Societies for Experimental Biology.

Muscle precursor cells injected into irradiated mdx mouse muscle persist after serial injury

J. Morgan, J. Gross, 1999, Muscle & nerve.

Myoblast transplantation in inherited myopathies.

D. Watt, J. Morgan, 1993, Molecular and cell biology of human diseases series.

Normal myogenic cells from newborn mice restore normal histology to degenerating muscles of the mdx mouse

E. Hoffman, T. Partridge, J. Morgan, 1990, The Journal of cell biology.

Mdx muscle grafts retain the mdx phenotype in normal hosts

T. Partridge, J. Morgan, G. Coulton, 1989, Muscle & nerve.

Molecular and genetic mapping of the mouse mdx locus.

N. Brockdorff, K. Davies, S. Forrest, 1988, Genomics.

Phosphorylase kinase activities in damaged mouse skeletal muscles

J. Morgan, 1988, Journal of the Neurological Sciences.

185th ENMC International Workshop: Stem/precursor cells as a therapeutic strategy for muscular dystrophies 3–5 June 2011, Naarden, The Netherlands

K. Patel, J. Morgan, 2012, Neuromuscular Disorders.

The altered expression of neurofilament in mouse models and patients with spinal muscular atrophy

F. Muntoni, L. Greensmith, Haiyan Zhou, 2021, Annals of clinical and translational neurology.

Partial correction of an inherited biochemical defect of skeletal muscle by grafts of normal muscle precursor cells

D. Watt, J. Morgan, J. Sloper, 1988, Journal of the Neurological Sciences.

CRISPR-mediated correction of skeletal muscle Ca2+ handling in a novel DMD patient-derived pluripotent stem cell model

F. Muntoni, Jihee Kim, N. Christoforou, 2022, Neuromuscular Disorders.

Satellite cells from dystrophic muscle retain regenerative capacity

J. Morgan, P. Zammit, L. Boldrin, 2015, Stem cell research.

Repeated low doses of morpholino antisense oligomer: an intermediate mouse model of spinal muscular atrophy to explore the window of therapeutic response.

F. Muntoni, Haiyan Zhou, J. Morgan, 2015, Human molecular genetics.

Contribution of Human Muscle-Derived Cells to Skeletal Muscle Regeneration in Dystrophic Host Mice

F. Muntoni, Shiwen Xu, J. Morgan, 2011, PloS one.

A novel high-throughput immunofluorescence analysis method for quantifying dystrophin intensity in entire transverse sections of Duchenne muscular dystrophy muscle biopsy samples

F. Muntoni, V. Sardone, C. Sewry, 2018, PloS one.

A New Extensively Characterised Conditionally Immortal Muscle Cell-Line for Investigating Therapeutic Strategies in Muscular Dystrophies

D. Wells, J. Morgan, S. Muses, 2011, PloS one.

Integrated Functions of Pax3 and Pax7 in the Regulation of Proliferation, Cell Size and Myogenic Differentiation

Robert B. White, V. Gnocchi, J. Morgan, 2009, PloS one.

Modulation of the host skeletal muscle niche for donor satellite cell grafting.

J. Morgan, L. Boldrin, 2013, Methods in molecular biology.

Donor Satellite Cell Engraftment is Significantly Augmented When the Host Niche is Preserved and Endogenous Satellite Cells are Incapacitated

F. Muntoni, J. Morgan, P. Zammit, 2012, Stem cells.

Human satellite cells: identification on human muscle fibres

J. Morgan, L. Boldrin, 2012, PLoS currents.

Tissue-specific Stem Cells

J. Morgan, L. Boldrin, 2022 .

Allografts of muscle precursor cells persist in the non-tolerized host

D. Watt, T. Partridge, J. Morgan, 1991, Neuromuscular Disorders.

Cell transplantation and gene therapy in muscular dystrophy.

T. Partridge, J. Morgan, 1992, BioEssays : news and reviews in molecular, cellular and developmental biology.

Long term survival of allografted muscle precursor cells following a limited period of treatment with cyclosporin A.

D. Watt, J. Morgan, T. Partridge, 1984, Clinical and experimental immunology.

The Satellite Cell in Male and Female, Developing and Adult Mouse Muscle: Distinct Stem Cells for Growth and Regeneration

J. Morgan, A. Neal, L. Boldrin, 2012, PloS one.

Long-term persistence and migration of myogenic cells injected into pre-irradiated muscles of mdx mice

T. Partridge, J. Morgan, C. Pagel, 1993, Journal of the Neurological Sciences.

Differential expression and secretion of alpha 1 anti-trypsin between direct DNA injection and implantation of transfected myoblast

Q. Lu, D. Wells, George Bou-Gharios, 1999, Gene Therapy.

Regeneration of skeletal muscle from transplanted immortalised myoblasts is oligoclonal

K. Woodward, T. Partridge, J. Morgan, 2004, Journal of Cell Science.

Stem Cell Function, Self-Renewal, and Behavioral Heterogeneity of Cells from the Adult Muscle Satellite Cell Niche

A. Petrie, T. Partridge, J. Morgan, 2005, Cell.

Stem cells to treat muscular dystrophies – Where are we?

F. Muntoni, J. Morgan, J. Meng, 2011, Neuromuscular Disorders.

The effect of calorie restriction on mouse skeletal muscle is sex, strain and time-dependent

J. Morgan, C. Beaver, A. Eddaoudi, 2017, Scientific Reports.

Genome Editing and Muscle Stem Cells as a Therapeutic Tool for Muscular Dystrophies

F. Muntoni, J. Morgan, V. Pini, 2017, Current Stem Cell Reports.

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study

J. Bourke, K. Bushby, F. Muntoni, 2011, The Lancet.

Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle.

I. Graham, F. Muntoni, L. Popplewell, 2007, Human gene therapy.

Dystromirs as Serum Biomarkers for Monitoring the Disease Severity in Duchenne Muscular Dystrophy

K. Bushby, F. Muntoni, A. Ferlini, 2013, PloS one.

Selective release of muscle-specific, extracellular microRNAs during myogenic differentiation

M. Turunen, M. Wood, I. Mäger, 2016, Human molecular genetics.

Direct Isolation of Satellite Cells for Skeletal Muscle Regeneration

Charlotte Collins, Ana Cumano, A. Cumano, 2005, Science.

Novel free-circulating and extracellular vesicle-derived miRNAs dysregulated in Duchenne muscular dystrophy.

V. Ricotti, F. Muntoni, L. Servais, 2020, Epigenomics.

A Population of Myogenic Stem Cells That Survives Skeletal Muscle Aging

T. Partridge, J. Morgan, P. Zammit, 2007, Stem cells.

Are Human and Mouse Satellite Cells Really the Same?

F. Muntoni, J. Morgan, L. Boldrin, 2010, The journal of histochemistry and cytochemistry : official journal of the Histochemistry Society.

Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts

L. Kunkel, E. Hoffman, J. Morgan, 1989, Nature.

Delivery of large transgene cassettes by foamy virus vector

J. Morgan, M. Mcclure, J. Meng, 2017, Scientific Reports.

Incorporation of donor muscle precursor cells into an area of muscle regeneration in the host mouse

D. Watt, T. Partridge, J. Morgan, 1982, Journal of the Neurological Sciences.

Altered Levels of MicroRNA-9, -206, and -132 in Spinal Muscular Atrophy and Their Response to Antisense Oligonucleotide Therapy

F. Muntoni, Haiyan Zhou, M. Scoto, 2016, Molecular therapy. Nucleic acids.

Ex vivo gene transfer using adenovirus-mediated full-length dystrophin delivery to dystrophic muscles

S. Kochanek, J. Yang, J. Huard, 1998, Gene Therapy.

Dual regulation of the AMP‐activated protein kinase provides a novel mechanism for the control of creatine kinase in skeletal muscle

D. Carling, D. Hardie, T. Partridge, 1998, The EMBO journal.

Autologous skeletal muscle derived cells expressing a novel functional dystrophin provide a potential therapy for Duchenne Muscular Dystrophy

F. Muntoni, Hanns Lochmüller, O. Danos, 2016, Scientific Reports.

Human Fetal Mesenchymal Stem Cells as Vehicles for Gene Delivery

Keelin O'Donoghue, Sailesh Kumar, J. Chan, 2005, Stem cells.

Myogenic cell proliferation and generation of a reversible tumorigenic phenotype are triggered by preirradiation of the recipient site

A. Fassati, J. D. Di Santo, D. Abraham, 2002, The Journal of cell biology.

Somatic reversion/suppression of the mouse mdx phenotype in vivo

Simon C Watkins, E. Hoffman, T. Partridge, 1990, Journal of the Neurological Sciences.

Characterisation of Stem Cells in Adult Mouse Muscle

J. Morgan, K. Blaveri, 2007 .

Patterns of repair of dystrophic mouse muscle: Studies on isolated fibers

T. Partridge, J. Morgan, L. Heslop, 1999, Developmental dynamics : an official publication of the American Association of Anatomists.

Dynamics of Myoblast Transplantation Reveal a Discrete Minority of Precursors with Stem Cell–like Properties as the Myogenic Source

T. Partridge, J. Morgan, C. Pagel, 1999, The Journal of cell biology.

Myostatin inhibition in combination with antisense oligonucleotide therapy improves outcomes in spinal muscular atrophy

F. Muntoni, G. Dickson, Haiyan Zhou, 2020, Journal of Cachexia, Sarcopenia and Muscle.

Histopathological Defects in Intestine in Severe Spinal Muscular Atrophy Mice Are Improved by Systemic Antisense Oligonucleotide Treatment

F. Muntoni, Haiyan Zhou, F. Catapano, 2016, PloS one.

A novel morpholino oligomer targeting ISS-N1 improves rescue of severe spinal muscular atrophy transgenic mice.

F. Muntoni, I. Eperon, K. Anthony, 2013, Human gene therapy.

Restoration of the dystrophin-associated glycoprotein complex after exon skipping therapy in Duchenne muscular dystrophy.

F. Muntoni, K. Anthony, V. Arechavala-Gomeza, 2012, Molecular therapy : the journal of the American Society of Gene Therapy.

Dystrophin expression and genotypic analysis of two cases of benign X linked myopathy (McLeod's syndrome).

A. Monaco, M. Schwartz, J. Morgan, 1990, Journal of medical genetics.

Cell and gene therapy in Duchenne muscular dystrophy.

J. Morgan, 1994, Human gene therapy.

The contribution of human synovial stem cells to skeletal muscle regeneration

Francesco Muntoni, Jinhong Meng, Jennifer E. Morgan, 2010, Neuromuscular Disorders.

Stem Cell Based Therapy for Muscular Dystrophies: Cell Types and Environmental Factors Influencing Their Efficacy

J. Morgan, H. Alameddine, 2012 .

A new immunodeficient mouse model for human myoblast transplantation.

A. Irintchev, A. Wernig, R. Cooper, 2001, Human gene therapy.

Erratum: Lentiviral vectors can be used for full-length dystrophin gene therapy

Francesco Muntoni, Simon N. Waddington, Steven J. Howe, 2017, Scientific Reports.

Lentiviral vectors can be used for full-length dystrophin gene therapy

Francesco Muntoni, Zeinab Asgarian, Jinhong Meng, 2017, Scientific Reports.

T Cell Responses to Dystrophin in a Natural History Study of Duchenne Muscular Dystrophy.

V. Ricotti, F. Muntoni, L. Servais, 2022, Human gene therapy.

Dystrophin quantification

F. Muntoni, K. Flanigan, K. Anthony, 2014, Neurology.

Exon skipping quantification by quantitative reverse-transcription polymerase chain reaction in Duchenne muscular dystrophy patients treated with the antisense oligomer eteplirsen.

K. Bushby, F. Muntoni, K. Anthony, 2012, Human gene therapy methods.

Antisense oligonucleotide-mediated exon skipping for Duchenne muscular dystrophy: progress and challenges.

F. Muntoni, K. Anthony, V. Arechavala-Gomeza, 2012, Current gene therapy.

Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse.

C. Mann, A. Cheng, S. Wilton, 2001, Proceedings of the National Academy of Sciences of the United States of America.

MRC Centre Neuromuscular Biobank (Newcastle and London): Supporting and facilitating rare and neuromuscular disease research worldwide

F. Muntoni, Hanns Lochmüller, M. Hanna, 2017, Neuromuscular Disorders.

Downregulation of miRNA-29, -23 and -21 in urine of Duchenne muscular dystrophy patients.

V. Ricotti, F. Muntoni, L. Servais, 2018, Epigenomics.

CD133+ cells derived from skeletal muscles of Duchenne muscular dystrophy patients have a compromised myogenic and muscle regenerative capability

F. Muntoni, J. Morgan, J. Meng, 2018, Stem cell research.

Dystrophin involvement in peripheral circadian SRF signalling

A. Bhomra, M. Bowerman, M. Falzarano, 2021, Life Science Alliance.

Dystrophin regulates peripheral circadian SRF signalling

A. Bhomra, M. Bowerman, M. Falzarano, 2021, bioRxiv.

Title Dystrophin regulates peripheral circadian SRF signalling Authors

A. Bhomra, M. Bowerman, M. Falzarano, 2021 .

The human desmin locus: gene organization and LCR-mediated transcriptional control.

J. Tam, S. Raguz, F. Grosveld, 2006, Genomics.

Expansion of revertant fibers in dystrophic mdx muscles reflects activity of muscle precursor cells and serves as an index of muscle regeneration

K. Davies, S. Takeda, T. Partridge, 2006, Journal of Cell Science.

Extracellular microRNAs are dynamic non-vesicular biomarkers of muscle turnover

I. Sargent, M. Wood, Y. Aoki, 2013, Nucleic acids research.

Regeneration after free muscle grafting in normal and dystrophic (mdx) mice

G. Maréchal, J. Morgan, T. Partridge, 1992, Journal of the Neurological Sciences.

Practical aspects of myoblast implantation: investigations on two inherited myopathies in animals.

J. Morgan, 1990, Advances in experimental medicine and biology.

Potentiation of myoblast transplantation by host muscle irradiation is dependent on the rate of radiation delivery

George Bou-Gharios, J. Morgan, J. Gross, 1999, Cell and Tissue Research.

Defects in Glycosylation Impair Satellite Stem Cell Function and Niche Composition in the Muscles of the Dystrophic Largemyd Mouse

Susan C. Brown, F. Muntoni, J. Hewitt, 2012, Stem cells.

Correspondence: Measuring dystrophin—faster is not necessarily better

F. Muntoni, V. Arechavala-Gomeza, J. Morgan, 2012, Nature Reviews Neurology.

Uncoordinated Transcription and Compromised Muscle Function in the Lmna-Null Mouse Model of Emery-Dreifuss Muscular Dystrophy

Robert B. White, Juliet A. Ellis, Yin-Biao Sun, 2011, PloS one.

CHAPTER 52 – MYOBLAST THERAPY

T. Partridge, J. Morgan, J. C. Cousins, 2000 .

Replication of myogenic cells with age, and myogenesis after experimental injury in mdx mouse muscle : quantitative autoradiographic studies

M. Grounds, T. Partridge, J. Morgan, 1992 .

Matrix Metalloproteinases and Tissue Inhibitor of Metalloproteinases in Inflammation and Fibrosis of Skeletal Muscles

J. Morgan, H. Alameddine, 2016, Journal of neuromuscular diseases.

Restoration of dystrophin expression using the Sleeping Beauty transposon

D. Wells, J. Morgan, S. Muses, 2011, PLoS currents.

Restoration of dystrophin expression using the Sleeping Beauty transposon.

D. Wells, J. Morgan, S. Muses, 2011, PLoS currents.

Irradiation dependent inflammatory response may enhance satellite cell engraftment

S. Torelli, J. Morgan, B. Doreste, 2020, Scientific Reports.

Multiple insights from myogenic cell transplants.

T. Partridge, J. Morgan, 2014, Human gene therapy.

Forced MyHCIIB expression following targeted genetic manipulation of conditionally immortalized muscle precursor cells.

M. Peckham, J. Morgan, A. Porter, 1999, Experimental cell research.

Myf5 expression in satellite cells and spindles in adult muscle is controlled by separate genetic elements.

P. Rigby, J. Carvajal, T. Partridge, 2004, Developmental biology.

Human Skeletal Muscle-derived CD133+ Cells Form Functional Satellite Cells After Intramuscular Transplantation in Immunodeficient Host Mice.

F. Muntoni, Hanns Lochmüller, J. Morgan, 2014, Molecular therapy : the journal of the American Society of Gene Therapy.

MyoD-induced reprogramming of human fibroblasts and urinary stem cells in vitro: protocols and their applications

S. Torelli, J. Morgan, R. Rossi, 2023, Frontiers in Physiology.

N. Romero, D. Mack, E. Zanoteli, 2020, Acta neuropathologica communications.

The effect of calorie restriction on mouse skeletal muscle is sex, strain and time-dependent

J. Morgan, C. Beaver, A. Eddaoudi, 2017, Scientific Reports.

The effect of the muscle environment on the regenerative capacity of human skeletal muscle stem cells

F. Muntoni, J. Morgan, R. Asfahani, 2015, Skeletal Muscle.

A high–throughput digital script for multiplexed immunofluorescent analysis and quantification of sarcolemmal and sarcomeric proteins in muscular dystrophies

F. Muntoni, F. Catapano, C. Sewry, 2020, Acta Neuropathologica Communications.

Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of-concept study

I. Graham, F. Muntoni, P. Nihoyannopoulos, 2009, The Lancet. Neurology.

Matrix Metalloproteinases and Tissue Inhibitor of Metalloproteinases in Inflammation and Fibrosis of Skeletal Muscles

J. Morgan, H. Alameddine, 2016, Journal of Neuromuscular Diseases.

Floyd, S.S. Jr. et al. Ex vivo gene transfer using adenovirus-mediated full-length dystrophin delivery to dystrophic muscles. Gene Ther. 5, 19-30

S. Kochanek, J. Huard, J. Morgan, 1998 .

Investigating the Impact of Delivery Routes for Exon Skipping Therapies in the CNS of DMD Mouse Models

A. Goyenvalle, L. García, J. Morgan, 2023, Cells.

Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study.

K. Bushby, F. Muntoni, K. Anthony, 2011, Lancet.