F. Mingozzi
发表
Kathleen A. Marshall,
G. Ying,
E. Stone,
2009,
The Lancet.
Kathleen A. Marshall,
M. Ashtari,
G. Ying,
2012,
Science Translational Medicine.
J. Rasko,
M. Kay,
J. Zehnder,
2006,
Nature Medicine.
Kathleen A. Marshall,
R. Hertle,
M. Maguire,
2008,
The New England journal of medicine.
M. Kay,
M. Valentine,
C. Morton,
2018,
Molecular therapy : the journal of the American Society of Gene Therapy.
A. D. De Groot,
S. Richards,
N. Dellas,
2020,
Bioanalysis.
K. High,
F. Mingozzi,
Federico Mingozzi,
2013,
Blood.
F. Mingozzi,
K. Kuranda,
2017
.
Jean Bennett,
Manzar Ashtari,
Kathleen A. Marshall,
2016,
The Lancet.
C. Casari,
O. Christophe,
P. Lenting,
2020,
EMBO molecular medicine.
P. Tak,
J. F. Wright,
F. Mingozzi,
2015,
PloS one.
F. Mingozzi,
O. Adjali,
Céline Vandamme,
2017,
Human gene therapy.
F. Mingozzi,
N. Junge,
2021,
Pediatric Liver Transplantation.
J. Rasko,
M. Ozelo,
X. Anguela,
2020,
Molecular therapy : the journal of the American Society of Gene Therapy.
C. Leborgne,
S. Boutin,
F. Mingozzi,
2019,
Cellular immunology.
H. Büning,
F. Mingozzi,
2015,
Front. Immunol..
J. F. Wright,
X. Anguela,
K. High,
2013,
Science Translational Medicine.
J. F. Wright,
J. Sommer,
B. Hauck,
2009,
Molecular therapy : the journal of the American Society of Gene Therapy.
E. Ayuso,
V. Haurigot,
J. Ruberte,
2013,
The Journal of clinical investigation.
Influence of Pre-existing Anti-capsid Neutralizing and Binding Antibodies on AAV Vector Transduction
G. Ronzitti,
Laetitia van Wittenberghe,
C. Leborgne,
2018,
Molecular therapy. Methods & clinical development.
F. Bernardi,
G. Marchetti,
C. Legnani,
2003,
Thrombosis and Haemostasis.
M. Kay,
M. Ozelo,
J. F. Wright,
2006
.
P. Laforêt,
G. Ronzitti,
F. Mingozzi,
2019,
Annals of translational medicine.
Z. Xiang,
H. Ertl,
Xiangyang Zhou,
2022,
Human gene therapy.
A. D. De Groot,
F. Mingozzi,
W. Martin,
2013,
Clinical & developmental immunology.
G. Ronzitti,
Laetitia van Wittenberghe,
F. Mingozzi,
2020,
Molecular therapy : the journal of the American Society of Gene Therapy.
B. Hyman,
T. Ragan,
E. Hudry,
2016,
Gene Therapy.
Piero Carninci,
S. Gustincich,
S. Zucchelli,
2019,
Molecular therapy : the journal of the American Society of Gene Therapy.
Laetitia van Wittenberghe,
F. Mingozzi,
B. Gjata,
2020,
EBioMedicine.
E. Malfatti,
P. Laforêt,
J. Vissing,
2021,
Neuromuscular Disorders.
C. Duyckaerts,
D. Klatzmann,
T. Maisonobe,
2014,
PloS one.
E. Malfatti,
N. Romero,
I. Nishino,
2019,
Acta Neuropathologica Communications.
X. Anguela,
G. Ronzitti,
Laetitia van Wittenberghe,
2021,
Nature Communications.
F. Mingozzi,
P. Colella,
2019,
Human gene therapy.
G. Ronzitti,
C. Leborgne,
T. Kishimoto,
2016
.
V. Arruda,
Shangzhen Zhou,
F. Mingozzi,
2015,
Blood.
Yuqin Wang,
R. Herzog,
K. High,
2003,
The Journal of clinical investigation.
F. Chapon,
G. Bassez,
D. Orlikowski,
2016,
Scientific Reports.
C. Leborgne,
F. Mingozzi,
P. Véron,
2015,
Human gene therapy methods.
D. Girelli,
F. Bernardi,
J. Rosing,
2000,
Thrombosis and Haemostasis.
F. Mingozzi,
F. Boisgérault,
2015,
Current gene therapy.
H. Ertl,
K. High,
P. Colosi,
2005,
Molecular therapy : the journal of the American Society of Gene Therapy.
D. Scott,
A. D. De Groot,
Valérie Ferreira,
2012,
Human vaccines & immunotherapeutics.
D. Scott,
Valérie Ferreira,
Yan Su,
2012
.
R. Herzog,
F. Mingozzi,
E. Dobrzynski,
2006,
Proceedings of the National Academy of Sciences of the United States of America.
V. Haurigot,
H. Stedman,
J. F. Wright,
2010,
Blood.
J. F. Wright,
B. Hauck,
K. High,
2009,
Molecular therapy : the journal of the American Society of Gene Therapy.
F. Bernardi,
C. Legnani,
G. Palareti,
2005,
Thrombosis and Haemostasis.
B. Kleinstiver,
J. Moon,
F. Mingozzi,
2020,
Scientific Reports.
Songtao Li,
G. Ronzitti,
C. Leborgne,
2019,
Molecular therapy. Methods & clinical development.
K. High,
F. Mingozzi,
2007,
Current gene therapy.
F. Mingozzi,
E. Basner-Tschakarjan,
2014,
Front. Immunol..
P. Tak,
K. High,
Shangzhen Zhou,
2012,
Gene Therapy.
V. Haurigot,
H. Stedman,
J. F. Wright,
2010,
Molecular therapy : the journal of the American Society of Gene Therapy.
L. D’Antiga,
G. Ronzitti,
T. Kishimoto,
2020,
Molecular therapy. Methods & clinical development.
C. Dunbar,
R. Donahue,
M. Metzger,
2012,
Molecular therapy : the journal of the American Society of Gene Therapy.
R. Herzog,
K. High,
F. Mingozzi,
2004,
Human gene therapy.
R. Herzog,
T. Nichols,
W. Xiao,
2004,
Blood.
R. Herzog,
K. High,
V. Arruda,
2001,
Molecular therapy : the journal of the American Society of Gene Therapy.
G. Ronzitti,
Laetitia van Wittenberghe,
C. Leborgne,
2021,
Science advances.
O. Christophe,
G. Ronzitti,
Laetitia van Wittenberghe,
2017,
Blood advances.
L. Valentino,
C. Négrier,
P. Monahan,
2021,
Journal of clinical medicine.
R. Herzog,
F. Mingozzi,
E. Dobrzynski,
2004,
Blood.
O. Christophe,
G. Ronzitti,
Laetitia van Wittenberghe,
2018,
Nature Communications.
J. F. Wright,
K. High,
V. Arruda,
2007,
Blood.
L. Zentilin,
M. Kay,
A. Muro,
2022,
Frontiers in Genome Editing.
Laetitia van Wittenberghe,
C. Leborgne,
F. Mingozzi,
2018,
Molecular therapy. Methods & clinical development.
J. Weisel,
M. Ellis,
D. Vaughan,
2020,
Research and practice in thrombosis and haemostasis.
F. Bernardi,
G. Castaman,
F. Mingozzi,
1998,
Blood.
G. Ronzitti,
F. Mingozzi,
2018,
Molecular therapy : the journal of the American Society of Gene Therapy.
K. High,
D. Sabatino,
F. Mingozzi,
2009,
Journal of medical virology.
D. Scott,
David Steven Scott,
S. Khoury,
2012,
Journal of Clinical Immunology.
M. Ott,
F. Mingozzi,
U. Baumann,
2015,
Journal of pediatric gastroenterology and nutrition.
D. Grimm,
R. McKenna,
M. Agbandje-McKenna,
2022,
Science advances.
J. Davoust,
J. Demengeot,
G. Ronzitti,
2019,
JCI insight.
G. Ronzitti,
C. Leborgne,
F. Mingozzi,
2018,
The Journal of clinical investigation.
D. Scott,
A. D. De Groot,
V. Haurigot,
2013,
Molecular therapy : the journal of the American Society of Gene Therapy.
H. Ertl,
R. Herzog,
A. Srivastava,
2013,
Blood.
A. Nienhuis,
J. Gray,
M. Valentine,
2011,
Molecular therapy : the journal of the American Society of Gene Therapy.
R. Herzog,
F. Mingozzi,
E. Dobrzynski,
2005,
Gene Therapy.
Songtao Li,
G. Ronzitti,
C. Leborgne,
2019,
Molecular therapy. Methods & clinical development.
E. Ayuso,
V. Haurigot,
F. Bosch,
2012,
Human gene therapy.
H. Waldmann,
Songtao Li,
C. Leborgne,
2015,
Human gene therapy.
F. Mingozzi,
J. Martinet,
O. Boyer,
2016,
Front. Immunol..
P. Fagone,
A. Nienhuis,
O. Christophe,
2014
.
P. Fagone,
A. Nienhuis,
O. Christophe,
2013,
Blood.
K. High,
A. Flake,
F. Mingozzi,
2012,
Blood.
A. Rötig,
P. de Lonlay,
F. Mingozzi,
2022,
Nature Communications.
S. Lope-Piedrafita,
F. Mingozzi,
M. Hirano,
2020,
EBioMedicine.
F. Mingozzi,
M. Hirano,
R. Martí,
2019,
Human Gene Therapy.
P. Bosma,
U. Beuers,
G. Ronzitti,
2020,
Molecular therapy. Methods & clinical development.
Laetitia van Wittenberghe,
C. Leborgne,
Y. Fromes,
2020,
Scientific Reports.
P. Bosma,
N. Brunetti‐Pierri,
L. D’Antiga,
2019,
Human gene therapy.
G. Comi,
E. Malfatti,
I. Richard,
2017,
Molecular therapy : the journal of the American Society of Gene Therapy.
Jean Bennett,
Gui-Shuang Ying,
Francesco Testa,
2009,
Molecular therapy : the journal of the American Society of Gene Therapy.
D. Scott,
S. Khoury,
W. Elyaman,
2012,
Journal of Clinical Immunology.
S. Lacroix-Desmazes,
X. Anguela,
G. Ronzitti,
2020,
Nature Medicine.
R. Herzog,
F. Mingozzi,
E. Dobrzynski,
2007,
Human gene therapy.
A. Contestabile,
G. Ronzitti,
G. Morelli,
2021,
Molecular therapy : the journal of the American Society of Gene Therapy.
Michael Recht,
Pratima Chowdary,
Deepak Raj,
2014,
The New England journal of medicine.
Pratima Chowdary,
Savita Rangarajan,
Cecilia Rosales,
2011,
The New England journal of medicine.
B. Schweighardt,
F. Mingozzi,
P. Véron,
2020,
Molecular therapy : the journal of the American Society of Gene Therapy.
K. High,
F. Mingozzi,
2011,
Nature Reviews Genetics.
Hojun Li,
Frederic D Bushman,
Nirav Malani,
2011,
Blood.
C. Négrier,
Y. Dargaud,
F. Mingozzi,
2019,
Thrombosis and Haemostasis.
M. Kay,
A. Nienhuis,
J. Gray,
2010
.
Marcela V Maus,
Hildegund C J Ertl,
Haiyan Jiang,
2007,
Nature Medicine.
L. Valentino,
X. Anguela,
M. Carr,
2018,
Blood.
J Montane,
E. Ayuso,
V. Haurigot,
2010,
Gene Therapy.
R. Herzog,
W. Xiao,
K. High,
2002,
Journal of Virology.
G. Ronzitti,
F. Mingozzi,
Federico Mingozzi,
2017,
Molecular therapy. Methods & clinical development.
F. Mingozzi,
Klaudia Kuranda,
Federico Mingozzi,
2020,
Molecular therapy : the journal of the American Society of Gene Therapy.
G. Ronzitti,
F. Mingozzi,
D. Gross,
2020,
Frontiers in Immunology.
P. Bosma,
G. Ronzitti,
A. Muro,
2018,
Molecular therapy. Methods & clinical development.
L. D’Antiga,
A. Muro,
F. Mingozzi,
2019,
Pediatric Hepatology and Liver Transplantation.
H. Büning,
F. Mingozzi,
2015
.
J. Rasko,
M. Recht,
X. Anguela,
2021,
The New England journal of medicine.
J. Golden,
J. Bennett,
K. High,
2010,
Science Translational Medicine.
O. Benveniste,
F. Mingozzi,
W. Mauhin,
2015,
JIMD reports.
K. High,
F. Mingozzi,
2011,
Nature Reviews Genetics.
Colin J. Chu,
G. Church,
A. Dick,
2021,
Science Translational Medicine.
H. Motaln,
F. Pagani,
S. Slaugenhaupt,
2018,
Human molecular genetics.
M. Pinotti,
G. Ronzitti,
Laetitia van Wittenberghe,
2016,
Molecular therapy. Nucleic acids.
F. Mingozzi,
M. Hirano,
R. Martí,
2019,
Human gene therapy.
F. Ducongé,
S. Tada,
G. Ronzitti,
2019,
Molecular therapy. Methods & clinical development.
P. Bosma,
G. Ronzitti,
Xiaoxiao Shi,
2020,
Molecular therapy. Methods & clinical development.
F. Bernardi,
F. Mingozzi,
E. Castoldi,
1998,
Blood.
P. Simioni,
A. Girolami,
F. Bernardi,
2001,
British journal of haematology.
M. Kay,
P. Laforêt,
G. Ronzitti,
2017,
Science Translational Medicine.
K. High,
F. Mingozzi,
2017,
Annual review of virology.
C. Mann,
E. Ayuso,
V. Haurigot,
2013,
Diabetes.
Etiena Basner-Tschakarjan,
M. Betts,
J. Kastelein,
2009,
Blood.
J. Sommer,
K. High,
L. Couto,
2006,
Blood.
J. Sommer,
K. High,
L. Couto,
2006
.
Z. Xiang,
H. Ertl,
R. Kurupati,
2019,
Molecular therapy : the journal of the American Society of Gene Therapy.
R. Grange,
A. Beggs,
D. Mack,
2017,
Molecular therapy : the journal of the American Society of Gene Therapy.
P. Bosma,
G. Ronzitti,
Laetitia van Wittenberghe,
2016,
Molecular therapy. Methods & clinical development.
Etiena Basner-Tschakarjan,
H. Ertl,
K. High,
2015,
Molecular therapy. Methods & clinical development.
O. Christophe,
P. de Bleser,
M. Y. Rincon,
2014,
Molecular therapy : the journal of the American Society of Gene Therapy.
J. Prieto,
G. González-Aseguinolaza,
Á. Vales,
2013,
PloS one.
H. Ertl,
R. Herzog,
A. Srivastava,
2013
.
M. Kay,
M. Ozelo,
J. F. Wright,
2006
.
N. Ross,
F. Mingozzi,
Kevin Y. Kim,
2022,
Frontiers in Immunology.
Laetitia van Wittenberghe,
C. Leborgne,
Y. Fromes,
2020,
Scientific Reports.
V. Haurigot,
J. Ruberte,
F. Bosch,
2015,
Human molecular genetics.
K. High,
Shangzhen Zhou,
F. Mingozzi,
2010,
Molecular therapy : the journal of the American Society of Gene Therapy.
J. Orange,
K. High,
Shangzhen Zhou,
2009,
The Journal of clinical investigation.
J. Rasko,
M. Kay,
J. Zehnder,
2006,
Nature Medicine.
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy
Thomas Voit,
Jean-Yves Hogrel,
Laurent Servais,
2017,
Nature Communications.
B. Hyman,
T. Ragan,
E. Hudry,
2016,
Gene Therapy.
B. Hyman,
T. Ragan,
E. Hudry,
2016,
Gene Therapy.
M. Blüher,
W. Bloch,
G. Ronzitti,
2017,
Hepatology.
E. Ayuso,
F. Bosch,
F. Mingozzi,
2010,
Current gene therapy.
J. Davoust,
I. Richard,
G. Ronzitti,
2019,
Molecular therapy. Methods & clinical development.
D. Gaudet,
K. High,
F. Mingozzi,
2008
.
F. Mingozzi,
G. Pavani,
E. Masat,
2013,
Discovery medicine.
J. Rasko,
H. Ertl,
K. High,
2006
.
J. F. Wright,
G. Acland,
C. Zeiss,
2008,
Molecular therapy : the journal of the American Society of Gene Therapy.
F. Bernardi,
G. Marchetti,
F. Mingozzi,
1997,
Thrombosis and Haemostasis.
D. Scott,
S. Khoury,
W. Elyaman,
2013,
The Journal of Immunology.
O. Christophe,
G. Ronzitti,
Laetitia van Wittenberghe,
2018,
Nature Communications.
F. Mingozzi,
2018,
Molecular therapy : the journal of the American Society of Gene Therapy.
F. Mingozzi,
R. Hardet,
2017,
Molecular therapy : the journal of the American Society of Gene Therapy.
F. Lamari,
D. Lacombe,
E. Hachulla,
2018,
Orphanet Journal of Rare Diseases.
Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor
C. Casari,
O. Christophe,
P. Lenting,
2021,
Gene Therapy.
E. Malfatti,
N. Romero,
I. Nishino,
2019,
Acta Neuropathologica Communications.
K. Cornetta,
J. Mahlangu,
S. Rangarajan,
2022,
Molecular therapy : the journal of the American Society of Gene Therapy.
G. Mariani,
F. Bernardi,
F. Mingozzi,
2001,
Haematologica.
S. Piletsky,
A. Garcia-Cruz,
E. Piletska,
2023,
Nanomedicine : nanotechnology, biology, and medicine.
P. Tak,
F. Mingozzi,
M. Vervoordeldonk,
2010
.
Songtao Li,
G. Ronzitti,
C. Leborgne,
2017,
Molecular therapy. Methods & clinical development.
D. Girelli,
F. Bernardi,
J. Rosing,
1999
.
K. High,
T. VandenDriessche,
M. Chuah,
2012
.
Kathleen A. Marshall,
M. Ashtari,
J. Bennett,
2016,
The Lancet.
M. Kay,
A. Nienhuis,
J. Gray,
2014,
The New England journal of medicine.
F. Bushman,
Nirav Malani,
K. High,
2011,
Blood.
F. Mingozzi,
2023
.
V. Haurigot,
Shangzhen Zhou,
F. Mingozzi,
2022
.
Kathleen A. Marshall,
O. Elci,
K. High,
2017
.
K. High,
Shangzhen Zhou,
F. Mingozzi,
2009
.
K. High,
F. Mingozzi,
W. Martin,
2010
.
C. Leborgne,
S. Boutin,
F. Mingozzi,
2019,
Cellular immunology.
M. Betts,
J. Kastelein,
K. High,
2009,
Blood.
P. Bosma,
U. Baumann,
N. Brunetti‐Pierri,
2023,
The New England journal of medicine.
K. High,
A. Flake,
F. Mingozzi,
2012,
Blood.
G. Ronzitti,
F. Mingozzi,
F. Collaud,
2023,
Journal of inherited metabolic disease.
K. High,
F. Mingozzi,
2009,
Nature Medicine.
A. Rötig,
P. de Lonlay,
A. Brassier,
2023,
Journal of inherited metabolic disease.
K. High,
F. Mingozzi,
2011,
Current gene therapy.
J. Golden,
J. Bennett,
K. High,
2010,
Science Translational Medicine.