P. Clemens
发表
K. Davies,
G. Dickson,
Annemieke Aartsma-Rus,
2011,
Molecular therapy : the journal of the American Society of Gene Therapy.
R. Finkel,
S. Pandya,
K. Kinnett,
2010,
The Lancet Neurology.
Michael A. Freitas,
J. Mendell,
P. Robbins,
2011,
Molecular medicine.
S. Kochanek,
A. Gambotto,
E. Feingold,
2001,
Molecular therapy : the journal of the American Society of Gene Therapy.
N. Joyce,
P. Clemens,
L. Hache,
2012,
Physical medicine and rehabilitation clinics of North America.
J. Watchko,
Juan Li,
Xiao Xiao,
2010,
Gene Therapy.
D. Lacomis,
P. Clemens,
S. Živković,
2012,
Journal of Neurology.
E. Hoffman,
A. Pestronk,
R. Abresch,
2020,
European Journal of Human Genetics.
P. Morel,
P. Clemens,
S. Eghtesad,
2009,
Immunology.
P. Robbins,
J. Watchko,
D. Guttridge,
2011,
Neurobiology of Disease.
E. Hoffman,
P. Clemens,
1996,
Current opinion in rheumatology.
A. Kanai,
W. D. de Groat,
L. Birder,
2001,
Proceedings of the National Academy of Sciences of the United States of America.
S. Jhunjhunwala,
S. Little,
P. Clemens,
2011,
Molecular medicine.
Simon C Watkins,
G. M. Wilson,
P. Robbins,
2018,
PLoS biology.
E. Hoffman,
A. Pestronk,
R. Abresch,
2017,
Nature Communications.
A. Pestronk,
P. Laforêt,
C. Morgan,
2010,
The New England journal of medicine.
J. Watchko,
P. Clemens,
E. Raggi,
2012,
Molecular medicine.
M. Tarnopolsky,
Y. Chien,
J. Charrow,
2021,
The Lancet Neurology.
E. Hoffman,
Y. Hathout,
J. N. van den Anker,
2019,
Scientific Reports.
Kristy Brown,
E. Hoffman,
Y. Hathout,
2016,
Scientific Reports.
P. Clemens,
L. Hache,
V. Morgenroth,
2012,
BoneKEy reports.
E. Hoffman,
W. Jusko,
J. N. van den Anker,
2020,
Journal of clinical pharmacology.
R. Finkel,
E. Hoffman,
Y. Hathout,
2018,
Pharmacological research.
B. Byrne,
A. Pestronk,
M. Tarnopolsky,
2021,
The Lancet Neurology.
P. Clemens,
S. Živković,
Saša A. Živković,
2015
.
E. Hoffman,
A. Pestronk,
R. Abresch,
2017,
The Lancet.
A. Pestronk,
J. Charrow,
H. Plotkin,
2012,
Molecular genetics and metabolism.
S. Jhunjhunwala,
S. Little,
P. Clemens,
2012,
Scientific Reports.
K. Campbell,
C. Caskey,
Y. Sunada,
1996,
Gene therapy.
E. Hoffman,
C. Spurney,
C. McDonald,
2018,
PLOS Currents.
P. Clemens,
E. Hoffman,
S. Takeda,
2021,
Journal of neuromuscular diseases.
Leaf Huang,
M. Nishikawa,
L. Huang,
2001,
Molecular therapy : the journal of the American Society of Gene Therapy.
S. Kochanek,
S. Choi,
P. Clemens,
1999,
Human gene therapy.
B. Burwinkel,
M. Vorgerd,
D. Pongratz,
2003,
European Journal of Human Genetics.
Simon C Watkins,
E. Hoffman,
S. Kochanek,
1997,
Human gene therapy.
C. Caskey,
P. Clemens,
K. Mitani,
1993,
JAMA.
P. Clemens,
Ryan L. Hanson,
Rakshita A. Charan,
2012
.
S. Kochanek,
E. Feingold,
Zhilong Jiang,
2002,
Molecular Therapy.
E. Hoffman,
M. Myerburg,
I. Kovesdi,
1999,
Human gene therapy.
E. Naylor,
P. Clemens,
H. Abdel-Hamid,
2016,
Muscle & nerve.
D. Lacomis,
P. Clemens,
S. Živković,
2002,
Muscle & nerve.
S. Kochanek,
P. Clemens,
M. Ontell,
2002,
Molecular therapy : the journal of the American Society of Gene Therapy.
E. Hoffman,
C. Zaidman,
A. Connolly,
2020,
JAMA neurology.
J. Watchko,
P. Clemens,
Z. Jiang,
2008,
Gene Therapy.
K. North,
L. Specht,
S. Iannaccone,
1996,
Neurology.
J. Vockley,
H. Homayoun,
D. Lacomis,
2011,
Neuromuscular Disorders.
C. Spurney,
L. Morgenroth,
H. Gordish-Dressman,
2014,
Muscle & nerve.
S. Kochanek,
P. Clemens,
R. Bilbao,
2005,
Gene Therapy.
Craig McDonald,
Frederic Shapiro,
Katharine Bushby,
2010,
The Lancet Neurology.
P. Clemens,
D. Reay,
S. Eghtesad,
2009,
Annals of neurology.
Jay J. Han,
R. Abresch,
A. Cnaan,
2013,
Muscle & nerve.
R. Gibbs,
M. de Andrade,
C. Caskey,
1991,
American journal of human genetics.
Xiao Xiao,
J. Huard,
B. Deasy,
2008
.
R. Finkel,
E. Hoffman,
F. Muntoni,
2022,
JAMA network open.
M. Barmada,
S. Dobrowolski,
E. Naylor,
2014,
Muscle & nerve.
Eric P. Hoffman,
Pat Furlong,
Craig McDonald,
2015,
Proceedings of the National Academy of Sciences.
Jay J. Han,
E. Hoffman,
R. Abresch,
2013,
Muscle & nerve.
P. Clemens,
B. M. Koppanati,
2010
.
P. Clemens,
B. M. Koppanati,
2009
.
C. Caskey,
S. Kochanek,
K. Mitani,
1996,
Proceedings of the National Academy of Sciences of the United States of America.
P. Robbins,
D. Guttridge,
J. Huard,
2010,
Gene Therapy.
Simon C Watkins,
D. Stolz,
P. Robbins,
2012,
The Journal of clinical investigation.
M. de Andrade,
C. Caskey,
R. Chakraborty,
1994,
Genomics.
P. Clemens,
Ryan L. Hanson,
Rakshita A. Charan,
2012,
FASEB journal : official publication of the Federation of American Societies for Experimental Biology.
S. Kochanek,
R. Kelly,
P. Clemens,
1997,
Proceedings of the National Academy of Sciences of the United States of America.
C. Caskey,
P. Clemens,
K. Mitani,
1993,
Philosophical transactions of the Royal Society of London. Series B, Biological sciences.
Amy L. Parkhill,
R. Moxley,
M. Mcdermott,
2017,
Neurology.
S. Pandya,
S. Apkon,
S. Hadjiyannakis,
2018,
The Lancet Neurology.
C. McDonald,
P. Clemens,
E. Hoffman,
2023,
Journal of neuromuscular diseases.
E. Hoffman,
Y. Hathout,
P. Clemens,
2020,
Human molecular genetics.
E. Hoffman,
A. Pestronk,
R. Abresch,
2020,
European Journal of Human Genetics.
R. Finkel,
E. Hoffman,
J. Mccall,
2019,
Neuromuscular Disorders.
J. Florence,
A. Kornberg,
A. Connolly,
2012,
Neurology.
C. Caskey,
P. Ward,
D. Bulman,
1992,
Neurology.
A. Pestronk,
A. Nicorici,
J. Florence,
2021,
CPT: pharmacometrics & systems pharmacology.
R. Finkel,
A. Pestronk,
E. Mazzone,
2019,
Journal of Pharmacokinetics and Pharmacodynamics.
A. Connolly,
C. Heier,
Yi-Wen Chen,
2020,
Journal of personalized medicine.
A. Cnaan,
A. Connolly,
Yi-Wen Chen,
2018,
Neurology.
R. Gibbs,
A. Pizzuti,
M. C. Edwards,
1991,
Nucleic acids research.
T. Wickham,
P. Roelvink,
P. Clemens,
2003,
Human gene therapy.
S. Kochanek,
J. Bergelson,
P. Clemens,
2003,
Gene Therapy.
A. Connolly,
S. Iannaccone,
D. Escolar,
2011,
Muscle & nerve.
A. Pestronk,
S. Subramony,
K. Patel,
2005,
Annals of neurology.
P. Clemens,
F. Duncan,
2001,
Current neurology and neuroscience reports.
H. Nakai,
P. Clemens,
Rakshita A. Charan,
2012,
Molecular medicine.
K. Wack,
D. Stolz,
P. Robbins,
2015,
Molecular medicine.
C. Caskey,
F. Graham,
P. Clemens,
1995,
Human gene therapy.
C. Caskey,
P. Clemens,
C. C. Lee,
1992
.
Long-Term Functional Efficacy and Safety of Viltolarsen in Patients with Duchenne Muscular Dystrophy
E. Hoffman,
C. Zaidman,
A. Connolly,
2022,
Journal of neuromuscular diseases.
E. Hoffman,
W. Jusko,
K. Nagaraju,
2019,
Journal of clinical pharmacology.
A. Pestronk,
R. Abresch,
J. Bodensteiner,
2017,
Neuromuscular Disorders.
E. Hoffman,
Y. Hathout,
S. Boca,
2016,
PloS one.
H. Nakai,
P. Clemens,
M. Epperly,
2010,
Gene therapy.
H. Nakai,
P. Clemens,
M. Epperly,
2010,
Gene Therapy.
S. Kochanek,
Chau‐Ching Liu,
N. Van Rooijen,
2004,
Molecular therapy : the journal of the American Society of Gene Therapy.
D. Escolar,
P. Clemens,
R. Leshner,
2001,
Muscle & nerve.
Y. Chien,
V. Kimonis,
N. Leslie,
2019,
Human mutation.
Zhilong Jiang,
P. Clemens,
2006,
FASEB journal : official publication of the Federation of American Societies for Experimental Biology.
C. Camacho,
T. Oury,
A. Weinberg,
2007,
Journal of autoimmunity.
B. Byrne,
A. Cnaan,
A. Connolly,
2020,
Muscle & nerve.
Efficacy and Safety of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease After 97 Weeks
Y. Chien,
B. Schoser,
S. Illarioshkin,
2023,
JAMA neurology.
P. Clemens,
E. Kang,
Y. Katsumata,
2011,
Arthritis and rheumatism.
P. Clemens,
E. Kang,
M. Soejima,
2012
.
R. Liu-Bryan,
W. Ridgway,
P. Clemens,
2013,
The Journal of Immunology.
R. Finkel,
N. Goemans,
A. Childs,
2022,
JAMA neurology.
R. Finkel,
E. Hoffman,
M. Ryan,
2020,
PLoS medicine.
A. Engel,
P. Clemens,
M. Yamamoto,
1991,
Neurology.
P. Clemens,
S. Eghtesad,
Lei Wang,
2011,
Immunobiology.
A. Pestronk,
A. Connolly,
S. Iannaccone,
2007,
Neuromuscular Disorders.
A. Engel,
P. Clemens,
Masahiko Yamamoto,
1990,
Annals of neurology.
P. Clemens,
E. Hoffman,
2021,
Annals of neurology.
C. Zaidman,
A. Connolly,
V. Rao,
2023,
Journal of neuromuscular diseases.
P. Clemens,
H. Abdel-Hamid,
2012,
Current opinion in neurology.
Feasibility and Reproducibility of Echocardiographic Measures in Children with Muscular Dystrophies.
A. Cnaan,
A. Connolly,
C. Spurney,
2015,
Journal of the American Society of Echocardiography : official publication of the American Society of Echocardiography.
A. Engel,
P. Clemens,
M. Kilimann,
1994
.
A. Engel,
P. Clemens,
M. Kilimann,
1994,
Human molecular genetics.
R. Liu-Bryan,
W. Ridgway,
P. Clemens,
2013
.
A. Pestronk,
J. Florence,
P. Laforêt,
2008,
Neuromuscular Disorders.
K. Wagner,
P. Clemens,
E. Vroom,
2018,
Pediatrics.
A. Pestronk,
A. Cnaan,
A. Kornberg,
2011,
Neurology.
Juan Li,
Xiao Xiao,
P. Clemens,
2005,
Human Gene Therapy.
S. Kochanek,
J. Huard,
J. Morgan,
1998
.
P. Clemens,
X. Xiao,
J. Li,
2009,
Gene Therapy.
P. Robbins,
S. Plevy,
J. Tilstra,
2007,
Biochemical Society transactions.
P. Clemens,
C. Bertoni,
B. M. Koppanati,
2014,
Methods in molecular biology.
Y. Chien,
B. Schoser,
S. Illarioshkin,
2021
.
P. Clemens,
A. Puwanant,
Diana A Madrid,
2023,
Muscle & nerve.
S. Kochanek,
G. Schiedner,
P. Clemens,
2001,
Current opinion in molecular therapeutics.
S. Kochanek,
J. Yang,
J. Huard,
1998,
Gene Therapy.
B. Dobkin,
K. Marder,
J. Long,
2020,
JAMA neurology.
A. Pestronk,
J. Charrow,
H. Plotkin,
2012,
Molecular genetics and metabolism.
K. Davies,
G. Dickson,
Annemieke Aartsma-Rus,
2011,
Molecular therapy : the journal of the American Society of Gene Therapy.
E. Naylor,
P. Clemens,
H. Abdel-Hamid,
2016,
Muscle & nerve.
Michael A. Freitas,
J. Mendell,
P. Robbins,
2011,
Molecular medicine.
N. Joyce,
P. Clemens,
L. Hache,
2012,
Physical medicine and rehabilitation clinics of North America.
R. Gibbs,
C. Caskey,
J. Chamberlain,
1991,
American journal of human genetics.