M. K. Parente

发表

High-resolution magnetic resonance microscopy and diffusion tensor imaging to assess brain structural abnormalities in the murine mucopolysaccharidosis VII model.

M. Kumar, S. Kim, S. Pickup, 2014, Journal of neuropathology and experimental neurology.

Dysregulation of Gene Expression in a Lysosomal Storage Disease Varies between Brain Regions Implicating Unexpected Mechanisms of Neuropathology

J. Wolfe, M. K. Parente, R. Rozen, 2012, PloS one.

Comparison of transfection conditions for a lentivirus vector produced in large volumes.

B. Karolewski, J. Wolfe, M. K. Parente, 2003, Human gene therapy.

Selective neurodegeneration in murine mucopolysaccharidosis VII is progressive and reversible

J. Trojanowski, V. Lee, M. Passini, 2002, Annals of neurology.

Integrated analysis of proteome and transcriptome changes in the mucopolysaccharidosis type VII mouse hippocampus.

S. Seeholzer, J. Wolfe, M. K. Parente, 2016, Molecular genetics and metabolism.

Sustained Production of β-Glucuronidase from Localized Sites after AAV Vector Gene Transfer Results in Widespread Distribution of Enzyme and Reversal of Lysosomal Storage Lesions in a Large Volume of Brain in Mucopolysaccharidosis VII Mice

James M. Wilson, J. Wolfe, M. K. Parente, 1999, Experimental Neurology.

High level expression and export of beta-glucuronidase from murine mucopolysaccharidosis VII cells corrected by a double-copy retrovirus vector.

W. Sly, M. Sands, J. Wolfe, 1995, Gene therapy.

Single Cell Analysis and Selection of Living Retrovirus Vector-corrected Mucopolysaccharidosis VII Cells Using a Fluorescence-activated Cell Sorting-based Assay for Mammalian β-Glucuronidase Enzymatic Activity*

G. Nolan, M. Roederer, L. Herzenberg, 1999, The Journal of Biological Chemistry.

Long-term AAV vector gene and protein expression in mouse brain from a small pan-cellular promoter is similar to neural cell promoters

M. Passini, J. Wolfe, N. Fraser, 2009, Gene Therapy.

Modification of multiple transcriptional regulatory elements in a Moloney murine leukemia virus gene transfer vector circumvents silencing in fibroblast grafts and increases levels of expression of the transferred enzyme

B. Foley, J. Wolfe, J. Pongubala, 2002, Gene Therapy.

Gene Transfer of Low Levels of β-Glucuronidase Corrects Hepatic Lysosomal Storage in a Large Animal Model of Mucopolysaccharidosis VII

M. Haskins, M. Sands, J. Reilly, 2000 .

Production of increased titer retrovirus vectors from stable producer cell lines by superinfection and concentration.

J. Wolfe, M. K. Parente, 1996, Gene therapy.

Expanded repertoire of AAV vector serotypes mediate unique patterns of transduction in mouse brain.

James M. Wilson, L. Vandenberghe, J. Wolfe, 2008, Molecular therapy : the journal of the American Society of Gene Therapy.

Bilateral single-site intracerebral injection of a nonpathogenic herpes simplex virus-1 vector decreases anxiogenic behavior in MPS VII mice

G. Griffin, R. Valentino, J. Wolfe, 2015, Molecular therapy. Methods & clinical development.