Alla Tsytsykova

Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease.

Jinkuk Kim, Annapurna Poduri, P Ellen Grant, 2019, The New England journal of medicine.

A modified γ-retrovirus vector for X-linked severe combined immunodeficiency.

Christopher Baum, David A. Williams, Gregory Hopkins, 2014, The New England journal of medicine.