D. Carbonaro

发表

of enzyme-replacement therapy and cytoreduction Gene therapy / bone marrow transplantation in ADA-deficient mice : roles

Michael L Kaufman, D. Gjertson, D. Kohn, 2012 .

In vivo transduction by intravenous injection of a lentiviral vector expressing human ADA into neonatal ADA gene knockout mice: a novel form of enzyme replacement therapy for ADA deficiency.

D. Kohn, F. Dorey, M. Blackburn, 2006, Molecular therapy : the journal of the American Society of Gene Therapy.

T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates

K. Weinberg, L. Barsky, G. Crooks, 1998, Nature Medicine.

Selective survival of peripheral blood lymphocytes in children with HIV-1 following delivery of an anti-HIV gene to bone marrow CD34(+) cells.

C. von Kalle, R. Koup, M. Betts, 2005, Molecular therapy : the journal of the American Society of Gene Therapy.

Lentivirus Mediated Correction of Artemis-Deficient Severe Combined Immunodeficiency.

A. Schambach, K. Cornetta, J. Puck, 2017, Human gene therapy.

The 24-Hour Time Budget of Przewalski Horses

K. Houpt, D. Carbonaro, L. Boyd, 1988 .

NIGHT-TIME BEHAVIOR OF STABLED AND PASTURED PERI-PARTURIENT PONIES

M. F. O'Connell, K. Houpt, T. Houpt, 1986 .

Behavioral and physiological responses of dairy goats to isolation

T. Friend, D. Carbonaro, G. R. Dellmeier, 1992, Physiology & Behavior.

High-resolution analysis of cytosine methylation in the 5ĺong terminal repeat of retroviral vectors.

D. Kohn, D. Carbonaro, P. Robbins, 1998, Human gene therapy.

Expression from second-generation feline immunodeficiency virus vectors is impaired in human hematopoietic cells

G. Nolan, J. Abkowitz, S. S. Case, 2002 .

Efficient Characterization of Retro‐, Lenti‐, and Foamyvector‐Transduced Cell Populations by High‐Accuracy Insertion Site Sequencing

S. Karlsson, H. Glimm, M. Wissler, 2003, Annals of the New York Academy of Sciences.

Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans.

Aaron R Cooper, O. Yang, D. Gjertson, 2012, Blood.

Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency.

Michael L Kaufman, Aaron R Cooper, K. Cornetta, 2014, Molecular therapy : the journal of the American Society of Gene Therapy.

Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonates

B. Aronow, M. Wissler, D. Kohn, 2003, Nature Medicine.

Altered reactivity of the rat adrenal medulla

F. Hall, D. Carbonaro, P. Vulliet, 1988, Brain Research Bulletin.

A clinical trial of retroviral-mediated transfer of a rev-responsive element decoy gene into CD34(+) cells from the bone marrow of human immunodeficiency virus-1-infected children.

C. Salata, C. Zhou, D. Kohn, 1999, Blood.

Gene therapy/bone marrow transplantation in ADA-deficient mice: roles of enzyme-replacement therapy and cytoreduction.

Michael L Kaufman, D. Gjertson, D. Kohn, 2012, Blood.

Expression from second-generation feline immunodeficiency virus vectors is impaired in human hematopoietic cells.

G. Nolan, J. Abkowitz, S. S. Case, 2002, Molecular therapy : the journal of the American Society of Gene Therapy.

Prolonged pancytopenia in a gene therapy patient with ADA-deficient SCID and trisomy 8 mosaicism: a case report.

K. Weinberg, M. Borchert, G. Crooks, 2007, Blood.

Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansion.

D. Kohn, D. Skelton, Tiejuan Mi, 2008, Blood.

immunologic reconstitution despite low levels of engraftment Neonatal bone marrow transplantation of ADA-deficient SCID mice

D. Kohn, D. Skelton, Tiejuan Mi, 2008 .

Neonatal gene therapy of MPS I mice by intravenous injection of a lentiviral vector.

R. Moats, H. Shimada, Hiroshi Kobayashi, 2005, Molecular therapy : the journal of the American Society of Gene Therapy.

Clinical efficacy of gene-modified stem cells in adenosine deaminase–deficient immunodeficiency

Barbara Engel, John Tse, David Gjertson, 2017, The Journal of clinical investigation.

Gene Therapy for Pediatric AIDS

J. Church, D. Kohn, G. Bauer, 2000, Annals of the New York Academy of Sciences.

Behavioral and physiological responses of dairy goats to food thwarting

T. Friend, D. Carbonaro, G. R. Dellmeier, 1992, Physiology & Behavior.

The 24-Hour Time Budget of P r z e w a l s k i Horses

K. Houpt, D. Carbonaro, L. Boyd, 2022 .

Immune Reconstitution After Gene Therapy (GTx) for Adenosine Deaminase Deficient Severe Combined Immune Deficiency (ADA-SCID)

C. Kesserwan, D. Kohn, L. Muul, 2009 .

Immunological and metabolic correction after lentiviral vector mediated haematopoietic stem cell gene therapy for ADA deficiency

K. Cornetta, D. Kohn, A. Thrasher, 2014 .

A clinical trial of retroviral-mediated transfer of a rev-responsive element decoy gene into CD34(+) cells from the bone marrow of human immunodeficiency virus-1-infected children.

D. Carbonaro, K. Kearns, I. Bahner, 1999, Blood.