Julie DiStefano-Pappas

Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial

Jean Bennett, Manzar Ashtari, Kathleen A. Marshall, 2016, The Lancet.

The Natural History of Inherited Retinal Dystrophy Due to Biallelic Mutations in the RPE65 Gene.

M. Larsen, B. Lorenz, O. Elci, 2019, American journal of ophthalmology.

Novel mobility test to assess functional vision in patients with inherited retinal dystrophies

Jean Bennett, Zi-Fan Yu, Kathleen A. Marshall, 2018, Clinical & experimental ophthalmology.

Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial

Kathleen A. Marshall, M. Ashtari, J. Bennett, 2016, The Lancet.

Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutatons: a follow-on phase 1 trial

Kathleen A. Marshall, O. Elci, K. High, 2017 .