P. Moneuse

Long‐term survival outcomes of patients with Niemann‐Pick disease type C receiving miglustat treatment: A large retrospective observational study

M. Patterson, O. Morand, R. Giugliani, 2020, Journal of inherited metabolic disease.

Treatment outcomes following continuous miglustat therapy in patients with Niemann-Pick disease Type C: a final report of the NPC Registry

M. Patterson, Daniel W. Rosenberg, M. Vanier, 2020, Orphanet Journal of Rare Diseases.

Methodological quality of meta‐analyses: matched‐pairs comparison over time and between industry‐sponsored and academic‐sponsored reports

A. Whitehead, S. Hollis, J. Cappelleri, 2013, Research synthesis methods.

Statistical approaches for conducting network meta‐analysis in drug development

Byron Jones, Joseph C Cappelleri, Patrick Moneuse, 2011, Pharmaceutical statistics.

A tool to assess the quality of a meta‐analysis

Sally Hollis, Julian P T Higgins, Peter W Lane, 2013, Research synthesis methods.

Statistical approaches for conducting network meta‐analysis in drug development

J. Cappelleri, B. Jones, J. Roger, 2011, Pharmaceutical statistics.