Simon N Waddington

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver.

Geoffrey Kemball-Cook, Jenny McIntosh, Yunyu Spence, 2006, Blood.

Oncogenesis following delivery of a nonprimate lentiviral gene therapy vector to fetal and neonatal mice.

Christof von Kalle, Niraja Dighe, Alaine T. Ruthe, 2005, Molecular therapy : the journal of the American Society of Gene Therapy.

The differentiation and engraftment potential of mouse hematopoietic stem cells is maintained after bio-electrospray.

Suwan N Jayasinghe, S. Jayasinghe, S. Waddington, 2010, The Analyst.

Stable gene transfer to muscle using non-integrating lentiviral vectors.

Luis Apolonia, Gerben Bouma, N. Philpott, 2007, Molecular therapy : the journal of the American Society of Gene Therapy.

Lentiviral vectors can be used for full-length dystrophin gene therapy

Francesco Muntoni, Zeinab Asgarian, Jinhong Meng, 2017, Scientific Reports.

Fetal gene therapy for neurodegenerative disease of infants

Kevin Mills, Arijit Biswas, Sebastian Brandner, 2018, Nature Medicine.