Matteo Bovolenta

Cationic PMMA nanoparticles bind and deliver antisense oligoribonucleotides allowing restoration of dystrophin expression in the mdx mouse.

Luciano Merlini, Paola Braghetta, Alessandra Ferlini, 2009, Molecular therapy : the journal of the American Society of Gene Therapy.

Exploiting the CRISPR/Cas9 system to study alternative splicing in vivo: application to titin.

Isabelle Richard, S. Henriques, I. Richard, 2016, Human molecular genetics.