S Tunis

Core outcome set for gene therapy in haemophilia: Results of the coreHEM multistakeholder project

G F Pierce, A. Iorio, D. Messner, 2018, Haemophilia : the official journal of the World Federation of Hemophilia.

From adaptive licensing to adaptive pathways: Delivering a flexible life‐span approach to bring new drugs to patients

W Goettsch, D Samaha, S. Schneeweiss, 2015, Clinical pharmacology and therapeutics.