Sarah Smith

111 Highly efficient multiplexed base editing enables development of universal CD7-targeting CAR-T Cells to treat T-ALL

Jason M. Gehrke, G. Ciaramella, Y. Poh, 2020, Journal for ImmunoTherapy of Cancer.

Long-Term Engraftment and Fetal Globin Induction upon BCL11A Gene Editing in Bone-Marrow-Derived CD34+ Hematopoietic Stem and Progenitor Cells

X. Yang, E. Rebar, F. Urnov, 2017, Molecular therapy. Methods & clinical development.

Conversion of HbS to Hb G-Makassar By Adenine Base Editing Is Compatible with Normal Hemoglobin Function

Nicole M. Gaudelli, M. Packer, I. Slaymaker, 2021, Blood.

Evaluation of Cytosine Base Editing and Adenine Base Editing as a Potential Treatment for Alpha-1 Antitrypsin Deficiency.

M. Packer, C. Mueller, B. Cafferty, 2022, Molecular therapy : the journal of the American Society of Gene Therapy.