J. Ramos

Gene Therapy of Skeletal Muscle Disorders Using Viral Vectors

J. Chamberlain, A. Arnett, J. Ramos, 2012 .

Micro-dystrophin Gene Therapy Partially Enhances Exercise Capacity in Older Adult mdx Mice

B. D. Rodgers, Yemeserach Bishaw, J. Ramos, 2019, Molecular therapy. Methods & clinical development.

Development of Novel Micro-dystrophins with Enhanced Functionality

James M. Allen, J. Chamberlain, K. Hollinger, 2019, Molecular therapy : the journal of the American Society of Gene Therapy.

Animal models of muscular dystrophy.

John K. Hall, J. Seto, J. Chamberlain, 2012, Progress in molecular biology and translational science.

Gene replacement therapies for duchenne muscular dystrophy using adeno-associated viral vectors.

J. Seto, J. Chamberlain, Lindsey A. Muir, 2012, Current gene therapy.

Targeting a therapeutic LIF transgene to muscle via the immune system ameliorates muscular dystrophy

Steven S. Welc, Ying Wang, J. Tidball, 2019, Nature Communications.

Evaluating Properties of Dystrophin and Delivery Methods of rAAV Gene Therapy for Duchenne Muscular Dystrophy

J. Ramos, 2014 .

Klotho gene silencing promotes pathology in the mdx mouse model of Duchenne muscular dystrophy.

N. Khanlou, M. Kuro-o, Steven S. Welc, 2016, Human molecular genetics.

Targeting a therapeutic LIF transgene to muscle via the immune system ameliorates muscular dystrophy

Steven S. Welc, J. Tidball, Ying Wang, 2019, Nature Communications.