K. Benenato

mRNA Therapy Improves Metabolic and Behavioral Abnormalities in a Murine Model of Citrin Deficiency.

C. Lukacs, L. Guey, P. Giangrande, 2019, Molecular therapy : the journal of the American Society of Gene Therapy.

Accelerated Blood Clearance of Lipid Nanoparticles Entails a Biphasic Humoral Response of B-1 Followed by B-2 Lymphocytes to Distinct Antigenic Moieties

K. Burke, C. Mihai, Joe J. Senn, 2019, ImmunoHorizons.

Systemic messenger RNA as an etiological treatment for acute intermittent porphyria

C. Lukacs, M. Alegre, L. Guey, 2018, Nature Medicine.

Optimization of Lipid Nanoparticles for Intramuscular Administration of mRNA Vaccines

Kimberly J. Hassett, M. Moore, C. Mihai, 2019, Molecular therapy. Nucleic acids.

A Novel Amino Lipid Series for mRNA Delivery: Improved Endosomal Escape and Sustained Pharmacology and Safety in Non-human Primates.

Örn Almarsson, C. Mihai, Joe J. Senn, 2018, Molecular therapy : the journal of the American Society of Gene Therapy.

Discovery of a Novel Amino Lipid That Improves Lipid Nanoparticle Performance through Specific Interactions with mRNA

K. Benenato, S. Sabnis, Timothy Salerno, 2021, Advanced Functional Materials.

Systemic mRNA Therapy for the Treatment of Fabry Disease: Preclinical Studies in Wild-Type Mice, Fabry Mouse Model, and Wild-Type Non-human Primates.

C. Lukacs, L. Guey, K. Burke, 2019, American journal of human genetics.

Dual mRNA therapy restores metabolic function in long-term studies in mice with propionic acidemia

C. Lukacs, L. Guey, C. Mihai, 2020, Nature Communications.

Systemic messenger RNA as an etiological treatment for acute intermittent porphyria

C. Lukacs, M. Alegre, L. Guey, 2018, Nature Medicine.