Marcelo Simon Sola

Prevalence and long-term monitoring of humoral immunity against adeno-associated virus in Duchenne Muscular Dystrophy patients.

C. Leborgne, S. Boutin, F. Mingozzi, 2019, Cellular immunology.

Influence of Pre-existing Anti-capsid Neutralizing and Binding Antibodies on AAV Vector Transduction

G. Ronzitti, Laetitia van Wittenberghe, C. Leborgne, 2018, Molecular therapy. Methods & clinical development.

Enhanced liver gene transfer and evasion of preexisting humoral immunity with exosome-enveloped AAV vectors.

O. Christophe, G. Ronzitti, Laetitia van Wittenberghe, 2017, Blood advances.

Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration

O. Christophe, G. Ronzitti, Laetitia van Wittenberghe, 2018, Nature Communications.

AAV Gene Transfer with Tandem Promoter Design Prevents Anti-transgene Immunity and Provides Persistent Efficacy in Neonate Pompe Mice

Laetitia van Wittenberghe, C. Leborgne, F. Mingozzi, 2018, Molecular therapy. Methods & clinical development.

Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression.

G. Comi, E. Malfatti, I. Richard, 2017, Molecular therapy : the journal of the American Society of Gene Therapy.

Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration

O. Christophe, G. Ronzitti, Laetitia van Wittenberghe, 2018, Nature Communications.

Prevalence and long-term monitoring of humoral immunity against adeno-associated virus in Duchenne Muscular Dystrophy patients.

C. Leborgne, S. Boutin, F. Mingozzi, 2019, Cellular immunology.