R. Fiori

发表

Intra‐arterial transplantation of HLA‐matched donor mesoangioblasts in Duchenne muscular dystrophy

M. Sormani, S. Benedetti, A. Tettamanti, 2016, EMBO molecular medicine.

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

L. Biasco, S. Galimberti, M. Valsecchi, 2019, The Lancet. Haematology.

Intra‐arterial transplantation of HLA‐matched donor mesoangioblasts in Duchenne muscular dystrophy

M. Sormani, S. Benedetti, A. Tettamanti, 2015, EMBO molecular medicine.

Multiple BM harvests in pediatric donors for thalassemic siblings: safety, efficacy and ethical issues

M. Roncarolo, R. Miniero, F. Ciceri, 2008, Bone Marrow Transplantation.

Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapy

A. Biffi, A. Aiuti, R. Miniero, 2019, Bone Marrow Transplantation.

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial

P. Rancoita, L. Naldini, M. Roncarolo, 2016, The Lancet.

High incidence of severe cyclosporine neurotoxicity in children affected by haemoglobinopaties undergoing myeloablative haematopoietic stem cell transplantation: early diagnosis and prompt intervention ameliorates neurological outcome

M. Roncarolo, C. Baldoli, A. Biffi, 2010, Italian Journal of Pediatrics.

Abnormalities of acid-base balance and predisposition to metabolic acidosis in Metachromatic Leukodystrophy patients.

I. Salvo, C. Lanzani, A. Biffi, 2015, Molecular genetics and metabolism.

Intra‐arterial transplantation of HLA‐matched donor mesoangioblasts in Duchenne muscular dystrophy

M. Sormani, S. Benedetti, A. Tettamanti, 2015, EMBO molecular medicine.