Francine M. Gregoire

Functionalized lipid-like nanoparticles for in vivo mRNA delivery and base editing

Luis A. Barrera, D. McComb, Xinfu Zhang, 2020, Science Advances.

Gene Editing Technologies to Target HBV cccDNA

F. Zoulim, B. Testoni, E. Smekalova, 2022, Viruses.

Biocompatible, Purified VEGF-A mRNA Improves Cardiac Function after Intracardiac Injection 1 Week Post-myocardial Infarction in Swine

K. Chien, S. Martinsson, L. Gan, 2018, Molecular therapy. Methods & clinical development.

Adenine base editing reduces misfolded protein accumulation and toxicity in alpha-1 antitrypsin deficient patient iPSC-hepatocytes

M. Packer, C. Villacorta-Martin, R. Werder, 2021, Molecular therapy : the journal of the American Society of Gene Therapy.

Evaluation of Cytosine Base Editing and Adenine Base Editing as a Potential Treatment for Alpha-1 Antitrypsin Deficiency.

M. Packer, C. Mueller, B. Cafferty, 2022, Molecular therapy : the journal of the American Society of Gene Therapy.