Megan M. Krogman

Transgenic inactivation of murine myostatin does not decrease the severity of disease in a model of Spinal Muscular Atrophy

C. Lorson, H. Rindt, M. L. Garcia, 2012, Neuromuscular Disorders.

Direct central nervous system delivery provides enhanced protection following vector mediated gene replacement in a severe model of spinal muscular atrophy.

C. Lorson, Megan M. Krogman, M. Shababi, 2012, Biochemical and biophysical research communications.

Decreasing disease severity in symptomatic, Smn(-/-);SMN2(+/+), spinal muscular atrophy mice following scAAV9-SMN delivery.

C. Lorson, E. Osman, Megan M. Krogman, 2012, Human gene therapy.