M. Vila

Effect of genetic background on the dystrophic phenotype in mdx mice.

C. Lutz, K. Nagaraju, T. Partridge, 2016, Human molecular genetics.

Myoblasts and macrophages are required for therapeutic morpholino antisense oligonucleotide delivery to dystrophic muscle

E. Hoffman, Y. Hathout, J. Jaiswal, 2017, Nature Communications.

Myoblasts and macrophages are required for therapeutic morpholino antisense oligonucleotide delivery to dystrophic muscle

E. Hoffman, Y. Hathout, J. Jaiswal, 2017, Nature Communications.

Elusive sources of variability of dystrophin rescue by exon skipping

Kristy Brown, E. Hoffman, Y. Hathout, 2015, Skeletal Muscle.

Mitochondria mediate cell membrane repair and contribute to Duchenne muscular dystrophy

Kristy Brown, Y. Hathout, J. Jaiswal, 2016, Cell Death and Differentiation.

Morpholino‐induced exon skipping stimulates cell‐mediated and humoral responses to dystrophin in mdx mice

E. Hoffman, Y. Hathout, Yi-Wen Chen, 2019, The Journal of pathology.

Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy.

K. Mamchaoui, V. Mouly, S. Takeda, 2017, Molecular therapy : the journal of the American Society of Gene Therapy.

TNF-α-Induced microRNAs Control Dystrophin Expression in Becker Muscular Dystrophy.

E. Hoffman, C. Angelini, C. Heier, 2015, Cell reports.

Effects of Chronic, Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy.

Y. Hathout, K. Nagaraju, J. N. van den Anker, 2021, Journal of neuromuscular diseases.

TNF-α-Induced microRNAs Control Dystrophin Expression in Becker Muscular Dystrophy.

E. Hoffman, C. Angelini, C. Heier, 2015, Cell reports.