F. Salerio

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

L. Biasco, S. Galimberti, M. Valsecchi, 2019, The Lancet. Haematology.

Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans

L. Biasco, A. Aiuti, M. Cicalese, 2018, Nature Medicine.

Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans

L. Biasco, A. Aiuti, M. Cicalese, 2018, Nature Medicine.

Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency.

C. Cancrini, P. Rancoita, C. Di Serio, 2024, Nature medicine.