I. Avedillo Díez

Multiple independent second‐site mutations in two siblings with somatic mosaicism for Wiskott–Aldrich syndrome

M. Ballmaier, K. Welte, M. Germeshausen, 2008, Clinical genetics.

Retroviral WASP gene transfer into human hematopoietic stem cells reconstitutes the actin cytoskeleton in myeloid progeny cells differentiated in vitro.

U. Pannicke, K. Schwarz, M. Ballmaier, 2006, Experimental Hematology.

Development of novel efficient SIN vectors with improved safety features for Wiskott-Aldrich syndrome stem cell based gene therapy.

A. Schambach, C. Klein, D. Zychlinski, 2011, Molecular pharmaceutics.