I. Savchenko

Effective Viral Delivery of Genetic Constructs to Neuronal Culture for Modeling and Gene Therapy of GNAO1 Encephalopathy

V. Loginov, V. I. Marina, S. Vassilieva, 2022, Molecular Biology.

Therapeutic potential of highly functional codon-optimized microutrophin for muscle-specific expression

V. Soldatov, D. Reshetov, S. Vassilieva, 2022, Scientific Reports.

Therapeutic potential of highly functional codon-optimized microutrophin for muscle-specific expression

V. Soldatov, D. Reshetov, S. Vassilieva, 2022, Scientific Reports.

CRISPR/Cas9-generated mouse model with humanizing single-base substitution in the Gnao1 for safety studies of RNA therapeutics

A. Deykin, S. Vassilieva, A. Polikarpova, 2023, Frontiers in Genome Editing.

In-Frame Deletion of Dystrophin Exons 8–50 Results in DMD Phenotype

D. Ivankov, I. Galkin, S. Vassilieva, 2023, International journal of molecular sciences.

CRISPR-Cas9 correction in the DMD mouse model is accompanied by upregulation of Dp71f protein

V. Soldatov, A. Deykin, M. Pokrovskii, 2023, Molecular therapy. Methods & clinical development.