J. Deniaud

发表

Assessment of adeno-associated virus gene therapies efficacy on acid alpha-glucosidase restoration and glycogen storage correction in cardiac muscle of Pompe disease mice using synchrotron infrared and ultraviolet microspectroscopies

C. Sandt, F. Jamme, C. Thorin, 2019, Journal of Spectral Imaging.

Efficient CNS targeting in adult mice by intrathecal infusion of single-stranded AAV9-GFP for gene therapy of neurological disorders

C. Ciron, P. Aubourg, M. Colle, 2017, Gene Therapy.

Intracerebral Gene Therapy Using AAVrh.10-hARSA Recombinant Vector to Treat Patients with Early-Onset Forms of Metachromatic Leukodystrophy: Preclinical Feasibility and Safety Assessments in Nonhuman Primates.

M. Souweidane, R. Crystal, I. Bièche, 2015, Human gene therapy. Clinical development.

Intracisternal delivery of AAV9 results in oligodendrocyte and motor neuron transduction in the whole central nervous system of cats

M. Colle, B. Joussemet, M. Ledevin, 2014, Gene Therapy.

Satellite cells fail to contribute to muscle repair but are functional in Pompe disease (glycogenosis type II)

T. Larcher, C. Ciron, M. Colle, 2018, Acta neuropathologica communications.

Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease

F. Jamme, M. Fusellier, C. Caillaud, 2017, Acta Neuropathologica Communications.

Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats

F. Rolling, M. Colle, S. Moreau, 2015, Gene Therapy.

Histopathologic Changes of the Ear in Canine Models of Mucopolysaccharidosis Types I and VII

M. Wyers, M. Colle, S. Moreau, 2011, Veterinary pathology.

Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?

T. Larcher, M. Fusellier, Kévin Marche, 2020, Molecular therapy. Methods & clinical development.

Satellite cells fail to contribute to muscle repair but are functional in Pompe disease (glycogenosis type II)

T. Larcher, C. Ciron, M. Colle, 2018, Acta neuropathologica communications.

Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease

F. Jamme, M. Fusellier, C. Caillaud, 2017, Acta neuropathologica communications.