D. Almarza

Tropism-modified AAV vectors overcome barriers to successful cutaneous therapy.

F. Larcher, M. Hallek, H. Büning, 2014, Molecular therapy : the journal of the American Society of Gene Therapy.

Risk assessment in skin gene therapy: viral–cellular fusion transcripts generated by proviral transcriptional read-through in keratinocytes transduced with self-inactivating lentiviral vectors

F. Larcher, F. Mavilio, R. Murillas, 2011, Gene Therapy.

Gene Editing for the Efficient Correction of a Recurrent COL7A1 Mutation in Recessive Dystrophic Epidermolysis Bullosa Keratinocytes

M. del Río, F. Larcher, H. Büning, 2016, Molecular therapy. Nucleic acids.

Identification of a novel, methylation-dependent, RUNX2 regulatory region associated with osteoarthritis risk

D. Deehan, L. Reynard, J. Loughlin, 2018, Human molecular genetics.

Keratinocyte cell lines derived from severe generalized recessive Epidermolysis Bullosa patients carrying a highly recurrent COL7A1 homozygous mutation: models to assess cell and gene therapies in vitro and in vivo

J. Cigudosa, S. Llames, M. del Río, 2013, Experimental dermatology.

Prioritization of PLEC and GRINA as Osteoarthritis Risk Genes Through the Identification and Characterization of Novel Methylation Quantitative Trait Loci

D. Deehan, L. Reynard, A. Skelton, 2019, Arthritis & rheumatology.

Genome editing for human osteoarthritis - a perspective.

M. Cucchiarini, J. Loughlin, D. Almarza, 2017, Osteoarthritis and cartilage.