M. Zieger

Airway smooth muscle dysfunction in Pompe (Gaa-/- ) mice.

B. Byrne, D. Fuller, M. ElMallah, 2017, American journal of physiology. Lung cellular and molecular physiology.

Understanding the Cephalic Eyes of Pulmonate Gastropods: A Review*

V. Meyer-Rochow, M. Zieger, Marina Zieger, 2008 .

The eye of the freshwater prosobranch gastropod Viviparus viviparus: ultrastructure, electrophysiology and behaviour

V. Meyer-Rochow, I. Vakoliuk, M. Zieger, 2006 .

Small molecule screen employing patient-derived iPS hepatocytes identifies LRRK2 as a novel therapeutic target for Alpha1 Antitrypsin Deficiency

C. Mueller, P. Khoshkenar, S. Blackford, 2021, bioRxiv.

Intralingual and Intrapleural AAV Gene Therapy Prolongs Survival in a SOD1 ALS Mouse Model

Robert H. Brown, C. Mueller, M. ElMallah, 2019, Molecular therapy. Methods & clinical development.

Liver-directed SERPINA1 gene therapy attenuates progression of spontaneous and tobacco smoke-induced emphysema in α1-antitrypsin null mice

T. Flotte, C. Mueller, F. Borel, 2022, Molecular therapy. Methods & clinical development.

Muscle-Directed Delivery of an AAV1 Vector Leads to Capsid-Specific T Cell Exhaustion in Nonhuman Primates and Humans

T. Flotte, C. Mueller, G. Gernoux, 2020, Molecular therapy : the journal of the American Society of Gene Therapy.

Systemic Delivery of AAVB1-GAA Clears Glycogen and Prolongs Survival in a Mouse Model of Pompe Disease.

B. Byrne, Angela L McCall, M. ElMallah, 2019, Human gene therapy.