Ukina R. Sanford

UvA-DARE ( Digital Academic Repository ) Strain background modifies phenotypes in the ATP 8 B 1-deficient mouse

L. Pawlikowska, Ś. Sen, Sohela Shah, 2010 .

Strain Background Modifies Phenotypes in the ATP8B1-Deficient Mouse

L. Pawlikowska, Ś. Sen, Sohela Shah, 2010, PloS one.

Lentivirus Mediated Correction of Artemis-Deficient Severe Combined Immunodeficiency.

A. Schambach, K. Cornetta, J. Puck, 2017, Human gene therapy.

Efficacy of broadly neutralizing monoclonal antibody PG16 in HIV-infected humanized mice.

T. Wrin, P. Joshi, E. Maidji, 2014, Virology.

Intrahepatic Cholestasis of Pregnancy (ICP) in U.S. Latinas and Chileans: Clinical features, Ancestry Analysis, and Admixture Mapping

E. Ziv, D. Hu, S. Huntsman, 2015, PloS one.

Early Outcome of a Phase I/II Clinical Trial (NCT03538899) of Gene-Corrected Autologous CD34+ Hematopoietic Cells and Low-Exposure Busulfan in Newly Diagnosed Patients with Artemis-Deficient Severe Combined Immunodeficiency (ART-SCID)

J. Puck, R. McIvor, H. Malech, 2020 .

Lentiviral Gene Therapy for Artemis-Deficient SCID.

J. Puck, J. Hilton, H. Malech, 2022, The New England journal of medicine.