T. Cimms

Content validity and ePRO usability of the BPI-sf and “worst pain” item with pleural and peritoneal mesothelioma

H. Gelhorn, A. Skalicky, S. Eremenco, 2018, Journal of Patient-Reported Outcomes.

Development Of A New Patient Reported Outcome (PRO) Measure For Community-Acquired Bacterial Pneumonia (CABP)

J. Powers, S. Hoffmann, J. Crawley, 2014 .

The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII.

V. Sutton, E. Martins, C. Whitley, 2020, Molecular genetics and metabolism.

Individual heat map assessments demonstrate vestronidase alfa treatment response in a highly heterogeneous mucopolysaccharidosis VII study population

C. Whitley, P. Harmatz, Raymond Y. Wang, 2019, JIMD reports.

The efficacy and safety of burosumab in two patients with cutaneous skeletal hypophosphatemia syndrome.

D. Hamilton, T. Carpenter, S. Krolczyk, 2022, Bone.

Reply to: Burosumab for Tumor‐Induced Osteomalacia: not Enough of a Good Thing

R. Kumar, F. Rauch, P. Miller, 2021, Journal of bone and mineral research : the official journal of the American Society for Bone and Mineral Research.

Burosumab for the Treatment of Tumor‐Induced Osteomalacia

R. Kumar, F. Rauch, P. Miller, 2020, Journal of bone and mineral research : the official journal of the American Society for Bone and Mineral Research.

Qualitative evaluation of the symptoms and quality of life impacts of long-chain fatty acid oxidation disorders

Chloe Johnson, A. Gater, T. Cimms, 2022, Therapeutic advances in endocrinology and metabolism.

Content validity and electronic PRO (ePRO) usability of the Lung Cancer Symptom Scale-Mesothelioma (LCSS-Meso) in mesothelioma patients

M. Mahoney, R. Gralla, H. Gelhorn, 2018, Supportive Care in Cancer.

The ORTHO BC-SAT – a satisfaction questionnaire for women using hormonal contraceptives

D. Patrick, M. Rothman, A. Friedman, 2006, Quality of Life Research.

An international cross-sectional survey to characterize the humanistic burden of creatine transporter deficiency

C. Evans, S. Blair, M. Brandabur, 2022, Future Rare Diseases.