N. Desmaris

发表

Early Neurodegeneration Progresses Independently of Microglial Activation by Heparan Sulfate in the Brain of Mucopolysaccharidosis IIIB Mice

D. Cheillan, M. Vanier, I. Maire, 2008, PloS one.

Improved Behavior and Neuropathology in the Mouse Model of Sanfilippo Type IIIB Disease after Adeno-Associated Virus-Mediated Gene Transfer in the Striatum

A. Cressant, R. Froissart, M. Vanier, 2004, The Journal of Neuroscience.

α-l-Iduronidase transport in neurites

J. Heard, J. Ausseil, Michaël Hocquemiller, 2006 .

Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.

D. Trono, E. Perret, J. Heard, 2000, Human gene therapy.

Prevention of neuropathology in the mouse model of hurler syndrome

C. Caillaud, M. Vanier, J. Heard, 2004, Annals of neurology.

Long-term and significant correction of brain lesions in adult mucopolysaccharidosis type VII mice using recombinant AAV vectors.

E. Perret, J. Heard, A. Bosch, 2000, Molecular therapy : the journal of the American Society of Gene Therapy.

Safe, efficient, and reproducible gene therapy of the brain in the dog models of Sanfilippo and Hurler syndromes.

S. Raoul, H. Petry, M. Tardieu, 2011, Molecular therapy : the journal of the American Society of Gene Therapy.

Gene therapy of the brain in the dog model of Hurler's syndrome

S. Raoul, B. Schwartz, N. Ferry, 2006, Annals of neurology.

Production and neurotropism of lentivirus vectors pseudotyped with lyssavirus envelope glycoproteins.

M. Prevost, P. Perrin, N. Tordo, 2001, Molecular therapy : the journal of the American Society of Gene Therapy.

alpha-L-Iduronidase transport in neurites.

J. Heard, J. Ausseil, Michaël Hocquemiller, 2006, Molecular Genetics and Metabolism.