L. Batista

Reversion of the biochemical defects in murine embryonic Sandhoff neurons using a bicistronic lentiviral vector encoding hexosaminidase α and β

E. Richard, A. Futerman, C. Caillaud, 2006 .

Partial phenotypic correction and immune tolerance induction to enzyme replacement therapy after hematopoietic stem cell gene transfer of α‐glucosidase in Pompe disease

E. Richard, C. Caillaud, L. Batista, 2009, The journal of gene medicine.

Correction of glycogenosis type 2 by muscle-specific lentiviral vector

E. Richard, C. Caillaud, L. Batista, 2008, In Vitro Cellular & Developmental Biology - Animal.

Induced secretion of β-hexosaminidase by human brain endothelial cells: A novel approach in Sandhoff disease?

P. Couraud, F. Miller, C. Caillaud, 2010, Neurobiology of Disease.

Modulation of glycogen synthesis by RNA interference: towards a new therapeutic approach for glycogenosis type II.

E. Richard, N. Raben, C. Caillaud, 2008, Human molecular genetics.

Reversion of the biochemical defects in murine embryonic Sandhoff neurons using a bicistronic lentiviral vector encoding hexosaminidase alpha and beta.

E. Richard, A. Futerman, C. Caillaud, 2006, Journal of neurochemistry.

Partial phenotypic correction and immune tolerance induction to enzyme replacement therapy after hematopoietic stem cell gene transfer of α‐glucosidase in Pompe disease

E. Richard, C. Caillaud, L. Batista, 2009, The journal of gene medicine.