Yoshitaka Shibata

Sustained fetal hemoglobin induction in vivo is achieved by BCL11A interference and coexpressed truncated erythropoietin receptor

B. Ryu, J. Tisdale, R. Donahue, 2021, Science Translational Medicine.

Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease

J. Tisdale, Selami Demirci, J. Haro-Mora, 2021, Molecular therapy. Methods & clinical development.