J. Wherley

发表

Potentially therapeutic levels of anti-sickling globin gene expression following lentivirus-mediated gene transfer in sickle cell disease bone marrow CD34+ cells.

Michael L Kaufman, D. Kohn, D. Persons, 2015, Experimental hematology.

Preclinical studies for a phase 1 clinical trial of autologous hematopoietic stem cell gene therapy for sickle cell disease.

Michael L Kaufman, Aaron R Cooper, E. Grassman, 2017, Cytotherapy.

Effect of Insulators on the Expression of betaAS3 in Lentiviral Gene Therapy for Sickle Cell Disease - eScholarship

J. Wherley, 2013 .

Gene Therapy of Genetic Diseases of Blood Cells

D. Kohn, G. Kuftinec, J. Wherley, 2013 .

b-globin gene transfer to human bone marrow for sickle cell disease

Michael L Kaufman, Aaron R Cooper, H. Meiselman, 2018 .

β-globin gene transfer to human bone marrow for sickle cell disease.

Michael L Kaufman, Aaron R Cooper, H. Meiselman, 2013, The Journal of clinical investigation.

The human ankyrin 1 promoter insulator sustains gene expression in a β-globin lentiviral vector in hematopoietic stem cells

Michael L Kaufman, Aaron R Cooper, D. Kohn, 2015, Molecular therapy. Methods & clinical development.

Modification of hematopoietic stem/progenitor cells with CD19-specific chimeric antigen receptors as a novel approach for cancer immunotherapy.

D. Elashoff, Andy Tu, D. Kohn, 2013, Human gene therapy.

Allelic exclusion and peripheral reconstitution by TCR transgenic T cells arising from transduced human hematopoietic stem/progenitor cells.

Michael L Kaufman, D. Baltimore, A. Ribas, 2013, Molecular therapy : the journal of the American Society of Gene Therapy.

Nonmyeloablative Conditioning Regimen to Increase Engraftment of Gene-modified Hematopoietic Stem Cells in Young Rhesus Monkeys.

D. Elashoff, D. Kohn, A. Tarantal, 2012, Molecular therapy : the journal of the American Society of Gene Therapy.

Index of Suspicion in the NurseryCase 1: Failure to Thrive in a 2-Week-Old BoyCase 2: Term Infant With Abdominal Distention and Bilious Emesis

J. Wherley, Ramya Keshavaram, Ryan Moore, 2014 .