John K Yoon

Genetically engineered microglia-like cells have therapeutic potential for neurodegenerative disease

C. Mason, L. Biasco, Robert N. Plasschaert, 2021, bioRxiv.

High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing

L. Biasco, Robert N. Plasschaert, Aimin Yan, 2022 .

Screening chimeric GAA variants in preclinicalstudy results in hematopoietic stem cell genetherapy candidate vectors for Pompe disease

A. Schambach, T. Maiwald, Zeenath Unnisa, 2022, Molecular Therapy. Methods & Clinical Development.

Screening chimeric GAA variants in preclinical study results in hematopoietic stem cell gene therapy candidate vectors for Pompe disease

A. Schambach, T. Maiwald, Zeenath Unnisa, 2022, Molecular therapy. Methods & clinical development.

Gene Therapy Developments for Pompe Disease

Zeenath Unnisa, N. P. van Til, Jeffrey W. Schindler, 2022, Biomedicines.

High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing

L. Biasco, Robert N. Plasschaert, Aimin Yan, 2022, Molecular therapy : the journal of the American Society of Gene Therapy.