S. Hartung

Correction of metabolic, craniofacial, and neurologic abnormalities in MPS I mice treated at birth with adeno-associated virus vector transducing the human alpha-L-iduronidase gene.

W. Low, R. McIvor, C. Whitley, 2004, Molecular therapy : the journal of the American Society of Gene Therapy.

Enzymatic correction and cross-correction of mucopolysaccharidosis type I fibroblasts by adeno-associated virus-mediated transduction of the alpha-L-iduronidase gene.

R. McIvor, C. Whitley, R. Reddy, 1999, Human gene therapy.

In vivo transduction of cerebellar Purkinje cells using adeno-associated virus vectors.

W. Low, R. McIvor, W. Kaemmerer, 2000, Molecular therapy : the journal of the American Society of Gene Therapy.

Craniofacial Abnormalities in a Murine Knock-Out Model of Mucopolysaccharidosis I H: A Computed Tomography and Anatomic Study

W. Low, C. Whitley, D. Pan, 2004, The Journal of craniofacial surgery.