B. C. Fernandez

Preclinical studies for a phase 1 clinical trial of autologous hematopoietic stem cell gene therapy for sickle cell disease.

Michael L Kaufman, Aaron R Cooper, E. Grassman, 2017, Cytotherapy.

Clinical efficacy of gene-modified stem cells in adenosine deaminase–deficient immunodeficiency

Barbara Engel, John Tse, David Gjertson, 2017, The Journal of clinical investigation.

Polyribosomes Are Molecular 3D Nanoprinters That Orchestrate the Assembly of Vault Particles

V. Kickhoefer, L. Rome, J. Mrázek, 2014, ACS nano.