Swati Singh

发表

Evaluation of persistence and fate of ex vivo edited-HSC modified with donor template and Its role in correcting Sickle Cell Disease

D. Rawlings, S. Lotti, S. Pattabhi, 2021, bioRxiv.

In Vivo Outcome of Homology-Directed Repair at the HBB Gene in HSC Using Alternative Donor Template Delivery Methods

A. Scharenberg, D. Rawlings, S. Lotti, 2019, Molecular therapy. Nucleic acids.

Intraosseous delivery of platelet-targeted factor VIII lentiviral vector in humanized NBSGW mice

D. Rawlings, H. Kiem, C. Miao, 2022, Blood advances.

Ex vivo engineered human plasma cells exhibit robust protein secretion and long-term engraftment in vivo

D. Rawlings, N. Camp, R. James, 2022, Nature Communications.

Ubiquitous high-level gene expression in hematopoietic lineages provides effective lentiviral gene therapy of murine Wiskott-Aldrich syndrome.

H. Ochs, B. Ryu, D. Rawlings, 2012, Blood.

Safe and Effective Gene Therapy for Murine Wiskott-Aldrich Syndrome Using an Insulated Lentiviral Vector

D. Liggitt, A. Nienhuis, D. Rawlings, 2016, Molecular therapy. Methods & clinical development.

Effective, safe, and sustained correction of murine XLA using a UCOE-BTK promoter-based lentiviral vector

B. Ryu, D. Rawlings, Joseph Pangallo, 2021, Molecular therapy. Methods & clinical development.

Efficient modification of CCR5 in primary human hematopoietic cells using a megaTAL nuclease and AAV donor template

A. Scharenberg, D. Rawlings, Jordan Jarjour, 2015, Science Translational Medicine.

Rapamycin relieves lentiviral vector transduction resistance in human and mouse hematopoietic stem cells.

B. Torbett, D. Rawlings, H. Kiem, 2014, Blood.

The Tec Kinase–Regulated Phosphoproteome Reveals a Mechanism for the Regulation of Inhibitory Signals in Murine Macrophages

A. Plebani, Alejandro Wolf-Yadlin, D. Rawlings, 2015, The Journal of Immunology.

A disease-associated PTPN22 variant promotes systemic autoimmunity in murine models.

R. Moon, D. Liggitt, Alejandro Wolf-Yadlin, 2013, The Journal of clinical investigation.

Engineering Protein-Secreting Plasma Cells by Homology-Directed Repair in Primary Human B Cells

D. Rawlings, I. Meitlis, R. James, 2017, Molecular therapy : the journal of the American Society of Gene Therapy.

Neutralizing Antibodies Protect against Oral Transmission of Lymphocryptovirus

A. McGuire, D. Rawlings, Yu-Hsin Wan, 2020, Cell reports. Medicine.

132. Targeting the BTK Locus in Primary Human Hematopoietic Cells with TALENs and AAV Donor Template

D. Rawlings, Iram Khan, King L. Hung, 2016 .

Efficient and sustained FOXP3 locus editing in hematopoietic stem cells as a therapeutic approach for IPEX syndrome

Iram Khan, Yuchi Honaker, Swati Singh, 2023, Molecular therapy. Methods & clinical development.