Yinan Zheng

Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy

Rachael A. Powis, Ewout J. N. Groen, Evangelia Karyka, 2016, JCI insight.

Restoration of SMN in Schwann cells reverses myelination defects and improves neuromuscular function in spinal muscular atrophy

Rachael A. Powis, Ewout J. N. Groen, D. Sherman, 2016, Human Molecular Genetics.

Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy

Catherina G. Becker, Thomas H. Gillingwater, Simon H. Parson, 2016, JCI insight.