Alice Rovai

In vivo adenine base editing reverts C282Y and improves iron metabolism in hemochromatosis mice

Q. Yuan, M. Ott, D. Grimm, 2022, Nature Communications.

Pathological mechanism and antisense oligonucleotide-mediated rescue of a non-coding variant suppressing factor 9 RNA biogenesis leading to hemophilia B

M. Ott, A. Goyenvalle, A. Tiede, 2020, PLoS genetics.

Ex Vivo/In vivo Gene Editing in Hepatocytes Using “All-in-One” CRISPR-Adeno-Associated Virus Vectors with a Self-Linearizing Repair Template

A. Balakrishnan, Q. Yuan, Z. Dai, 2019, iScience.