David A. Williams

发表

CTC1 Mutations in a patient with dyskeratosis congenita

Rachel B. Keller, Suneet Agarwal, I. Hofmann, 2012, Pediatric blood & cancer.

Diagnosis and treatment of pediatric acquired aplastic anemia (AAA): An initial survey of the North American Pediatric Aplastic Anemia Consortium (NAPAAC)

S. Corey, T. Olson, A. Bertuch, 2014, Pediatric blood & cancer.

Concise Review: Lessons Learned From Clinical Trials of Gene Therapy in Monogenic Immunodeficiency Diseases

David A. Williams, A. Thrasher, David A. Williams, 2014, Stem cells translational medicine.

Highly efficient therapeutic gene editing of human hematopoietic stem cells

Chunyan Ren, Luca Pinello, Luca Biasco, 2019, Nature Medicine.

Prolonged Inhibition ofO6-Methylguanine DNA Methyltransferase in Human Tumor Cells by O6-Benzylguanine In Vitro and In Vivo

L. Erickson, E. Kreklau, C. Kurpad, 1999 .

Protection of hematopoietic cells against combined O6-benzylguanine and chloroethylnitrosourea treatment by mutant forms of O6-methylguanine DNA methyltransferase

R. Maze, C. Kurpad, L. Erickson, 2000, Bone Marrow Transplantation.

Lentiviral gene therapy for X-linked chronic granulomatous disease

Luca Biasco, Adrian J. Thrasher, David A. Williams, 2020, Nature Medicine.

GENE THERAPY: CURRENT STATUS AND FUTURE DIRECTIONS

J. Apperley, David A. Williams, 1990, British journal of haematology.

Flow cytometric assay for direct quantification of neutrophil extracellular traps in blood samples

C. Harris, K. Martinod, D. Wagner, 2015, American journal of hematology.

Genetic deletion of the GATA1‐regulated protein α‐synuclein reduces oxidative stress and nitric oxide synthase levels in mature erythrocytes

David A. Williams, D. Selkoe, M. LaVoie, 2014, American journal of hematology.

Transient neonatal hemolytic anemia due to the novel gamma globin gene mutation HBG2:C.290T>C, p.Leu97Pro (hemoglobin Wareham)

D. Chui, Hong‐yuan Luo, F. Wachter, 2022, Pediatric blood & cancer.

Validation of a small molecule inhibitor of PDE6D-RAS interaction with favorable anti-leukemic effects

A. Anighoro, C. Harris, Haiming Xu, 2022, Blood Cancer Journal.

Gene editing without ex vivo culture evades genotoxicity in human hematopoietic stem cells

Shondra M. Pruett-Miller, J. Joung, V. Pattanayak, 2023, bioRxiv.

Validation of a small molecule inhibitor of PDE6D-RAS interaction with potent anti-leukemic effects

A. Anighoro, C. Harris, Haiming Xu, 2022, bioRxiv.

Response to correspondence: Flow cytometric quantification of neutrophil extracellular traps: Limitations of the methodological approach by Ciepiela et al.

David A. Williams, M. Gavillet, David A. Williams, 2016, American journal of hematology.

Critical Variables affecting clinical-grade production of the self-inactivating gamma-retroviral vector for the treatment of X-linked severe combined immunodeficiency

A. Schambach, D. Williams, M. Cavazzana‐Calvo, 2012, Gene Therapy.