M. Manvell

An immunocytochemical assay to detect human CFTR expression following gene transfer.

A. Nairn, D. Porteous, R. Gray, 2009, Molecular and cellular probes.

Physico-chemical analysis of cationic liposome–DNA complexes (lipoplexes) with respect to in vitro and in vivo gene delivery efficiency

Andrew D. Miller, L. Stewart, E. Alton, 2001 .

Characterisation of LMD virus-like nanoparticles self-assembled from cationic liposomes, adenovirus core peptide μ (mu) and plasmid DNA

F. Booy, N. Lemoine, A. Miller, 2002, Gene Therapy.

Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial

Steve Cunningham, Joseph Jacob, Sarah Sheard, 2015 .

A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator ( CFTR) gene therapy in patients with cystic fibrosis

A. Nicholson, D. Hansell, A. Maclean, 2016 .

Limitations of the murine nose in the development of nonviral airway gene transfer.

D. Porteous, Charanjit Singh, R. Scheule, 2010, American journal of respiratory cell and molecular biology.

Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial

A. Nicholson, D. Hansell, A. Maclean, 2015, The Lancet. Respiratory medicine.

Safety and adverse events

A. Nicholson, D. Hansell, A. Maclean, 2016 .