Jill Pesayco Salvador

Krabbe disease successfully treated via monotherapy of intrathecal gene therapy.

C. Vite, E. Bongarzone, D. Ory, 2020, The Journal of clinical investigation.

AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease).

C. Vite, E. Bongarzone, D. Ory, 2018, Human gene therapy.