Tai-Ping Zhang

Optimization of self-complementary AAV vectors for liver-directed expression results in sustained correction of hemophilia B at low vector dose.

R. Samulski, T. van Dyke, C. Yin, 2008, Molecular therapy : the journal of the American Society of Gene Therapy.

Creation of a mouse expressing defective human factor IX.

P. Monahan, D. Stafford, D. Jin, 2004, Blood.

Transgene expression levels and kinetics determine risk of humoral immune response modeled in factor IX knockout and missense mutant mice

J. Frelinger, P. Monahan, D. Jin, 2007, Gene Therapy.