Congsheng Cheng

Haplotyping SNPs for allele-specific gene editing of the expanded huntingtin allele using long-read sequencing

B. Davidson, A. Dürr, Kai Wang, 2022, HGG advances.

High-fidelity SaCas9 identified by directional screening in human cells

Shuang Li, Feng Gu, Jinyu Wu, 2020, PLoS biology.

Elucidation of transcriptome-wide microRNA binding sites in human cardiac tissues by Ago2 HITS-CLIP

Beverly L. Davidson, Ryan M Spengler, B. Davidson, 2016, Nucleic acids research.

Efficient Human Genome Editing Using SaCas9 Ribonucleoprotein Complexes.

Feng Gu, Junzhao Zhao, R. Deng, 2019, Biotechnology journal.

In vivo SELEX for Identification of Brain-penetrating Aptamers

Mark A Behlke, B. Davidson, M. Behlke, 2013, Molecular therapy. Nucleic acids.

The long non-coding RNA NEAT1 is elevated in polyglutamine repeat expansion diseases and protects from disease gene-dependent toxicities

Ryan M Spengler, B. Davidson, S. Ramachandran, 2018, Human molecular genetics.

Targeting ABCB4 using mRNA-LNP for the treatment of rare liver diseases

Shangzhong Li, Morag H. Stewart, S. Chiang, 2023, bioRxiv.

Mapping PTBP2 binding in human brain identifies SYNGAP1 as a target for therapeutic splice switching

J. A. Maguire, E. Waxman, E. Heller, 2023, Nature communications.