Robert A Madumba

CRISPR-Cas9-Mediated Correction of the 1.02 kb Common Deletion in CLN3 in Induced Pluripotent Stem Cells from Patients with Batten Disease.

E. Stone, B. Tucker, E. Burnight, 2018, The CRISPR journal.

Using Patient-Specific Induced Pluripotent Stem Cells and Wild-Type Mice to Develop a Gene Augmentation-Based Strategy to Treat CLN3-Associated Retinal Degeneration.

E. Stone, B. Tucker, E. Burnight, 2016, Human gene therapy.

CRISPR-Cas9-Mediated Correction of the 1.02 kb Common Deletion in CLN3 in Induced Pluripotent Stem Cells from Patients with Batten Disease.

B. Tucker, Joseph C. Giacalone, L. A. Wiley, 2018, The CRISPR journal.