C. Makepeace

The incidence of hydrocephalus among patients with and without spinal muscular atrophy (SMA): Results from a US electronic health records study

I. Bhan, S. Eaton, A. Dilley, 2021, Orphanet Journal of Rare Diseases.

Comparative All-Cause Mortality Among a Large Population of Patients with Spinal Muscular Atrophy Versus Matched Controls

I. Bhan, S. Eaton, V. Kupelian, 2021, Neurology and Therapy.

Efficacy and safety of fumaric acid esters in young patients aged 10–17 years with moderate‐to‐severe plaque psoriasis: a randomized, double‐blinded, placebo‐controlled trial *

T. Gambichler, H. Hamm, A. Tsianakas, 2020, The British journal of dermatology.

DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results

R. Finkel, J. Day, M. Ryan, 2023, Journal of neuromuscular diseases.