Thais Watkins

The gRNA vector level determines the outcome of systemic AAV CRISPR therapy for Duchenne muscular dystrophy.

Chady H Hakim, Shi-jie Chen, D. Duan, 2022, Human gene therapy.

Dwarf Open Reading Frame (DWORF) Gene Therapy Ameliorated Duchenne Muscular Dystrophy Cardiomyopathy in Aged mdx Mice

D. Duan, Xiufang Pan, Y. Yue, 2023, Journal of the American Heart Association.

The implication of hinge 1 and hinge 4 in micro-dystrophin gene therapy for Duchenne muscular dystrophy.

D. Duan, N. Wasala, Y. Yue, 2022, Human gene therapy.