F. Wilkes

Discovery of 2-arylbenzoxazoles as upregulators of utrophin production for the treatment of Duchenne muscular dystrophy.

G. Wynne, K. Davies, R. Pye, 2011, Journal of medicinal chemistry.

Discovery and SAR of 2-arylbenzotriazoles and 2-arylindazoles as potential treatments for Duchenne muscular dystrophy.

G. Wynne, R. Pye, S. Wren, 2011, Bioorganic & Medicinal Chemistry Letters.

Analysis of factor VIII mediated suppression of lentiviral vector titres

P. Radcliffe, K. Mitrophanous, S. Kingsman, 2008, Gene Therapy.

Stable gene transfer to the nervous system using a non-primate lentiviral vector

A. Kingsman, Soonsang Yoon, N. Mazarakis, 1999, Gene Therapy.

Rabies virus glycoprotein pseudotyping of lentiviral vectors enables retrograde axonal transport and access to the nervous system after peripheral delivery.

A. Kingsman, E. Carter, R. Barber, 2001, Human molecular genetics.

Transduction patterns of pseudotyped lentiviral vectors in the nervous system.

N. Mazarakis, M. Azzouz, L. Walmsley, 2004, Molecular therapy : the journal of the American Society of Gene Therapy.

Lentivector-mediated SMN replacement in a mouse model of spinal muscular atrophy.

U. Monani, N. Mazarakis, M. Azzouz, 2004, The Journal of clinical investigation.

Daily Treatment with SMTC1100, a Novel Small Molecule Utrophin Upregulator, Dramatically Reduces the Dystrophic Symptoms in the mdx Mouse

K. Davies, S. Wren, A. De Luca, 2011, PloS one.