Mary E. Jacobs

Screening chimeric GAA variants in preclinicalstudy results in hematopoietic stem cell genetherapy candidate vectors for Pompe disease

A. Schambach, T. Maiwald, Zeenath Unnisa, 2022, Molecular Therapy. Methods & Clinical Development.

Screening chimeric GAA variants in preclinical study results in hematopoietic stem cell gene therapy candidate vectors for Pompe disease

A. Schambach, T. Maiwald, Zeenath Unnisa, 2022, Molecular therapy. Methods & clinical development.